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- [1] AAV-mediated gene therapy produces fertile offspring in the Lhcgr-deficient mouse model of Leydig cell failureCELL REPORTS MEDICINE, 2022, 3 (11)Xia, Kai论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaWang, Fulin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaLai, Xingqiang论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 8, Cardiovasc Dept, Shenzhen 518033, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaDong, Lin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaLuo, Peng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaZhang, Suyuan论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaYang, Cuifeng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaChen, Hong论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaMa, Yuanchen论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaHuang, Weijun论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaOu, Wangsheng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Zhong Shan Ophthalm Ctr, State Key Lab Ophthalmol, Guangzhou 510000, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaLi, Yuyan论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaFeng, Xin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaYang, Bin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaLiu, Congyuan论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaLei, Zhenmin论文数: 0 引用数: 0 h-index: 0机构: Univ Louisville, Dept OB GYN & Womens Hlth, Sch Med, Louisville, KY 40292 USA Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaTu, Xiang'an论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaKe, Qiong论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaMao, Frank Fuxiang论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Zhong Shan Ophthalm Ctr, State Key Lab Ophthalmol, Guangzhou 510000, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaDeng, Chunhua论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R ChinaXiang, Andy Peng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou 510080, Guangdong, Peoples R China Sun Yat sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou 510080, Guangdong, Peoples R China
- [2] AAV-mediated gene therapy restores natural fertility and improves physical function in the Lhcgr-deficient mouse model of Leydig cell failureCELL PROLIFERATION, 2024, 57 (09)Zhang, Suyuan论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaYang, Bin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaShen, Xiaoting论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Affiliated Hosp 1, Reprod Med Ctr, Key Lab Reprod Med Guangdong Prov, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaChen, Hong论文数: 0 引用数: 0 h-index: 0机构: Shenzhen Qianhai Shekou Free Trade Zone Hosp, Ctr Stem Cells Translat Med, Shenzhen, Guangdong, Peoples R China Chinese Acad Sci, Brain Cognit & Brain Dis Inst, Shenzhen Inst Adv Technol, Shenzhen, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaWang, Fulin论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaTan, Zhipeng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaOu, Wangsheng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Zhong Shan Ophthalm Ctr, State Key Lab Ophthalmol, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaYang, Cuifeng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaLiu, Congyuan论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaPeng, Hao论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaLuo, Peng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Affiliated Hosp 1, Reprod Med Ctr, Key Lab Reprod Med Guangdong Prov, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaPeng, Limei论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaLei, Zhenmin论文数: 0 引用数: 0 h-index: 0机构: Univ Louisville, Sch Med, Dept OB GYN & Womens Hlth, Louisville, KY USA Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaYan, Sunxing论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Cellgenes Biotechnol Co Ltd, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaWang, Tao论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaKe, Qiong论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaDeng, Chunhua论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Affiliated Hosp 1, Dept Urol & Androl, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaXiang, Andy Peng论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Key Lab Stem Cells & Tissue Engn,Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R ChinaXia, Kai论文数: 0 引用数: 0 h-index: 0机构: Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Guangzhou, Guangdong, Peoples R China Sun Yat Sen Univ, Natl Local Joint Engn Res Ctr Stem Cells & Regener, Zhongshan Sch Med, Key Lab Stem Cells & Tissue Engn,Minist Educ, Guangzhou 510080, Guangdong, Peoples R China Sun Yat Sen Univ, Ctr Stem Cell Biol & Tissue Engn, Key Lab Stem Cells & Tissue Engn, Minist Educ, Guangzhou, Guangdong, Peoples R China
- [3] AAV-mediated gene therapy in a mouse model of sialidosisMOLECULAR GENETICS AND METABOLISM, 2023, 138 (02) : 129 - 130van de Vlekkert, Diantha论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAHu, Huimin论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAWeesner, Jason A.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAGomero, Elida M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAd'Azzo, Alessandra论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USA
- [4] Effective AAV-mediated gene therapy in a mouse model of ethylmalonic encephalopathyEMBO MOLECULAR MEDICINE, 2012, 4 (09) : 1008 - 1014Di Meo, Ivano论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyAuricchio, Alberto论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Div Med Genet, Dept Pediat, Naples, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyLamperti, Costanza论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyBurlina, Alberto论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Pediat, Div Inherited Metab Dis, Padua, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyViscomi, Carlo论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyZeviani, Massimo论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy
- [5] AAV-Mediated Gene Replacement Therapy in Mouse Model of Tuberous SclerosisMOLECULAR THERAPY, 2015, 23 : S78 - S78Prabhakar, Shilpa论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAZhang, Xuan论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAGoto, June论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, Dept Med, Translat Med Div, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USARamesh, Vijaya论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Dept Neurol, Gene Therapy Ctr, Worcester, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USABronson, Roderick论文数: 0 引用数: 0 h-index: 0机构: MGH, Ctr Human Genet Res, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAChen, John W.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Rodent Histopathol Core Facil, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAStemmer-Rachamimov, Anat O.论文数: 0 引用数: 0 h-index: 0机构: MGH, Ctr Syst Biol, Boston, MA USA MGH, Dept Radiol, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAKwiatkowski, David J.论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USABreakefield, Xandra O.论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USA
- [6] AAV-mediated gene therapy in central nervous system of dystrophin-Dp71 deficient mouseNEUROMUSCULAR DISORDERS, 2017, 27 : S174 - S175Rendon, A.论文数: 0 引用数: 0 h-index: 0机构: Inst Vis, Paris, France Inst Vis, Paris, FranceVacca, O.论文数: 0 引用数: 0 h-index: 0机构: Neurosci Paris Saclay Inst, Orsay, France Inst Vis, Paris, FranceVaillend, C.论文数: 0 引用数: 0 h-index: 0机构: Neurosci Paris Saclay Inst, Orsay, France Inst Vis, Paris, France
- [7] The Potential of AAV-Mediated Gene Targeting for Gene and Cell Therapy ApplicationsCurrent Stem Cell Reports, 2015, 1 (1) : 16 - 22Alexander I.E.论文数: 0 引用数: 0 h-index: 0机构: Gene Therapy Research Unit, Children’s Medical Research Institute and The Children’s Hospital at Westmead, Locked Bag 23, Wentworthville, 2145, NSW Discipline of Paediatrics and Child Health, The University of Sydney, Sydney, 2145, NSW Gene Therapy Research Unit, Children’s Medical Research Institute, 214 Hawkesbury Road, Westmead, 2145, NSW Gene Therapy Research Unit, Children’s Medical Research Institute and The Children’s Hospital at Westmead, Locked Bag 23, Wentworthville, 2145, NSWRussell D.W.论文数: 0 引用数: 0 h-index: 0机构: Department of Medicine, University of Washington, Seattle, WA Department of Biochemistry, University of Washington, Seattle, WA Gene Therapy Research Unit, Children’s Medical Research Institute and The Children’s Hospital at Westmead, Locked Bag 23, Wentworthville, 2145, NSW
- [8] AAV-mediated gene therapy for retinal disorders: from mouse to manGENE THERAPY, 2008, 15 (11) : 849 - 857Buch, P. K.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Ophthalmol, Div Mol Therapy, London EC1V 9EL, EnglandBainbridge, J. W.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Ophthalmol, Div Mol Therapy, London EC1V 9EL, EnglandAli, R. R.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Ophthalmol, Div Mol Therapy, London EC1V 9EL, England UCL, Inst Ophthalmol, Div Mol Therapy, London EC1V 9EL, England
- [9] AAV-mediated gene therapy for retinal disorders: from mouse to manGene Therapy, 2008, 15 : 849 - 857P K Buch论文数: 0 引用数: 0 h-index: 0机构: UCL Institute of Ophthalmology and UCL/Moorfields Eye Hospital Biomedical Research Centre for Ophthalmology,Division of Molecular TherapyJ W Bainbridge论文数: 0 引用数: 0 h-index: 0机构: UCL Institute of Ophthalmology and UCL/Moorfields Eye Hospital Biomedical Research Centre for Ophthalmology,Division of Molecular TherapyR R Ali论文数: 0 引用数: 0 h-index: 0机构: UCL Institute of Ophthalmology and UCL/Moorfields Eye Hospital Biomedical Research Centre for Ophthalmology,Division of Molecular Therapy
- [10] AAV-Mediated Gene Therapy in Mouse Models of Recessive Retinal DegenerationCURRENT MOLECULAR MEDICINE, 2012, 12 (03) : 316 - 330Pang, J. -J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R China Univ Florida, Dept Ophthalmol, Coll Med, Gainesville, FL 32610 USA Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaLei, L.论文数: 0 引用数: 0 h-index: 0机构: Zhongshan Univ, Zhongshan Ophthalm Ctr, Guangzhou, Guangdong, Peoples R China Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaDai, X.论文数: 0 引用数: 0 h-index: 0机构: Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R China Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaShi, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Coll Med, Gainesville, FL 32610 USA Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaLiu, X.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Coll Med, Gainesville, FL 32610 USA Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaDinculescu, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Coll Med, Gainesville, FL 32610 USA Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R ChinaMcDowell, J. H.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Ophthalmol, Coll Med, Gainesville, FL 32610 USA Hosp Eye, Sch Ophthalmol & Optometry, Wenzhou Med Coll, Wenzhou, Peoples R China