AAV-mediated gene therapy in a mouse model of sialidosis

被引：0
|
作者：
van de Vlekkert, Diantha [1 ]
Hu, Huimin [1 ]
Weesner, Jason A. [1 ]
Gomero, Elida M. [1 ]
d'Azzo, Alessandra [1 ]
机构：
[1] St Jude Childrens Res Hosp, Genet, Memphis, TN USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2023年 / 138卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2022.107342
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
359
引用
收藏
页码：129 / 130
页数：2
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