AAV-Mediated Gene Replacement Therapy in Mouse Model of Tuberous Sclerosis

被引：0

作者：

Prabhakar, Shilpa ^{[1
]}

Zhang, Xuan ^{[1
]}

Goto, June ^{[1
]}

Sena-Esteves, Miguel ^{[2
]}

Ramesh, Vijaya ^{[3
]}

Bronson, Roderick ^{[4
]}

Chen, John W. ^{[5
]}

Stemmer-Rachamimov, Anat O. ^{[6
,7
]}

Kwiatkowski, David J. ^{[1
]}

Breakefield, Xandra O. ^{[1
]}

机构：

[1] MGH, Neurol & Radiol, Charlestown, MA 02115 USA

[2] Brigham & Womens Hosp, Dept Med, Translat Med Div, Boston, MA USA

[3] UMass Med Sch, Dept Neurol, Gene Therapy Ctr, Worcester, MA USA

[4] MGH, Ctr Human Genet Res, Boston, MA USA

[5] Harvard Univ, Sch Med, Rodent Histopathol Core Facil, Boston, MA USA

[6] MGH, Ctr Syst Biol, Boston, MA USA

[7] MGH, Dept Radiol, Boston, MA USA

来源：

MOLECULAR THERAPY | 2015年 / 23卷

关键词：

D O I：

10.1016/S1525-0016(16)33801-1

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

196

引用

页码：S78 / S78

页数：1

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