AAV-Mediated Gene Replacement Therapy in Mouse Model of Tuberous Sclerosis

被引：0
|
作者：
Prabhakar, Shilpa [1 ]
Zhang, Xuan [1 ]
Goto, June [1 ]
Sena-Esteves, Miguel [2 ]
Ramesh, Vijaya [3 ]
Bronson, Roderick [4 ]
Chen, John W. [5 ]
Stemmer-Rachamimov, Anat O. [6 ,7 ]
Kwiatkowski, David J. [1 ]
Breakefield, Xandra O. [1 ]
机构：
[1] MGH, Neurol & Radiol, Charlestown, MA 02115 USA
[2] Brigham & Womens Hosp, Dept Med, Translat Med Div, Boston, MA USA
[3] UMass Med Sch, Dept Neurol, Gene Therapy Ctr, Worcester, MA USA
[4] MGH, Ctr Human Genet Res, Boston, MA USA
[5] Harvard Univ, Sch Med, Rodent Histopathol Core Facil, Boston, MA USA
[6] MGH, Ctr Syst Biol, Boston, MA USA
[7] MGH, Dept Radiol, Boston, MA USA
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
10.1016/S1525-0016(16)33801-1
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
196
引用
收藏
页码：S78 / S78
页数：1
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