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- [1] AAV-Mediated Gene Replacement Therapy in Mouse Model of Tuberous Sclerosis[J]. MOLECULAR THERAPY, 2015, 23 : S78 - S78Prabhakar, Shilpa论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAZhang, Xuan论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAGoto, June论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USASena-Esteves, Miguel论文数: 0 引用数: 0 h-index: 0机构: Brigham & Womens Hosp, Dept Med, Translat Med Div, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USARamesh, Vijaya论文数: 0 引用数: 0 h-index: 0机构: UMass Med Sch, Dept Neurol, Gene Therapy Ctr, Worcester, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USABronson, Roderick论文数: 0 引用数: 0 h-index: 0机构: MGH, Ctr Human Genet Res, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAChen, John W.论文数: 0 引用数: 0 h-index: 0机构: Harvard Univ, Sch Med, Rodent Histopathol Core Facil, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAStemmer-Rachamimov, Anat O.论文数: 0 引用数: 0 h-index: 0机构: MGH, Ctr Syst Biol, Boston, MA USA MGH, Dept Radiol, Boston, MA USA MGH, Neurol & Radiol, Charlestown, MA 02115 USAKwiatkowski, David J.论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USABreakefield, Xandra O.论文数: 0 引用数: 0 h-index: 0机构: MGH, Neurol & Radiol, Charlestown, MA 02115 USA MGH, Neurol & Radiol, Charlestown, MA 02115 USA
- [2] AAV-mediated gene therapy in a mouse model of sialidosis[J]. MOLECULAR GENETICS AND METABOLISM, 2023, 138 (02) : 129 - 130van de Vlekkert, Diantha论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAHu, Huimin论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAWeesner, Jason A.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAGomero, Elida M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USAd'Azzo, Alessandra论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Genet, Memphis, TN USA St Jude Childrens Res Hosp, Genet, Memphis, TN USA
- [3] AAV-mediated Gene Replacement Therapy is Beneficial in Unverricht-Lundborg Disease Mouse Model[J]. AMERICAN JOURNAL OF PATHOLOGY, 2021, 191 (10 S): : S2 - S2Gumusgoz, Emrah论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USAKasiri, Sahba论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USAWu, Jun论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USADear, Matthew论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USAChen, Xin论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USAMinassian, Berge论文数: 0 引用数: 0 h-index: 0机构: Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA
- [4] Effective AAV-mediated gene therapy in a mouse model of ethylmalonic encephalopathy[J]. EMBO MOLECULAR MEDICINE, 2012, 4 (09) : 1008 - 1014Di Meo, Ivano论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyAuricchio, Alberto论文数: 0 引用数: 0 h-index: 0机构: Univ Naples Federico II, Telethon Inst Genet & Med TIGEM, Naples, Italy Univ Naples Federico II, Div Med Genet, Dept Pediat, Naples, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyLamperti, Costanza论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyBurlina, Alberto论文数: 0 引用数: 0 h-index: 0机构: Univ Padua, Dept Pediat, Div Inherited Metab Dis, Padua, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyViscomi, Carlo论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, ItalyZeviani, Massimo论文数: 0 引用数: 0 h-index: 0机构: Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy Fdn Carlo Besta Inst Neurol IRCCS, Unit Mol Neurogenet, Milan, Italy
- [5] Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID[J]. HUMAN MOLECULAR GENETICS, 2017, 26 (08) : 1535 - 1551Roca, Carles论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainMotas, Sandra论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainMarco, Sara论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainRibera, Albert论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainSanchez, Victor论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainSanchez, Xavier论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainBertolin, Joan论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainLeon, Xavier论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainPerez, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainGarcia, Miguel论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainVillacampa, Pilar论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Anim Hlth & Anat, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainPujol, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainHaurigot, Virginia论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, SpainBosch, Fatima论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain Univ Autonoma Barcelona, Dept Biochem & Mol Biol, Sch Vet Med, Bellaterra 08193, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Barcelona 08036, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Edifici H, E-08193 Bellaterra, Spain
- [6] AAV-mediated gene therapy to treat mucopolysaccharidosis type IVA in a new mouse model of the disease[J]. HUMAN GENE THERAPY, 2019, 30 (11) : A172 - A172Sanchez, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainBertolin, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainRibera, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainSanchez, X.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainMarco, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainMotas, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainPerez, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainRoca, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainElias, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainGarcia, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainLeon, X.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainHaurigot, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainRuberte, J.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Anim Hlth & Anat, Sch Vet Med, Barcelona, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, SpainBosch, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Barcelona, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Univ Autonoma Barcelona, Ctr Anim Biotechnol & Gene Therapy, Barcelona, Spain
- [7] Development of AAV Mediated Gene Therapy Approach for Usher Syndrome Type 2[J]. MOLECULAR THERAPY, 2023, 31 (04) : 636 - 637Chekuri, Anil论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USAWang, Weiwei论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USAVandenberghe, Luk H.论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Boston, MA USA Schepens Eye Res Inst, Boston, MA USA
- [8] AAV-Mediated Gene Therapy to Treat Mucopolysaccharidosis Type IVA in a New Morquio a Mouse Model[J]. MOLECULAR THERAPY, 2020, 28 (04) : 492 - 492Sanchez, Victor论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainBertolin, Joan论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainRibera, Albert论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainSanchez, Xavier论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainMarco, Sara论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainMotas, Sandra论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainPerez, Jennifer论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainRoca, Carles论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainElias, Gemma论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainGarcia, Miquel论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainLeon, Xavier论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainHaurigot, Virginia论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainRuberte, Jesus论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Anim Hlth & Anat, Cerdanyola Del Valles, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, SpainBosch, Fatima论文数: 0 引用数: 0 h-index: 0机构: Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain Univ Autonoma Barcelona, Biochem & Mol Biol, Cerdanyola Del valles, Spain Ctr Invest Biomed Red Diabet & Enfermedades Metab, Madrid, Spain Ctr Anim Biotechnol & Gene Therapy CBATEG, Cerdanyola Del valles, Spain
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- [10] Miniaturization of Usher Syndrome Type 2A ene for AAV Mediated Gene Therapy[J]. MOLECULAR THERAPY, 2021, 29 (04) : 270 - 270Wang, Weiwei论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Grousbeck Gene Therapy Ctr, Boston, MA USAFlorea, Michael论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Grousbeck Gene Therapy Ctr, Boston, MA USAVandenberghe, Luk H.论文数: 0 引用数: 0 h-index: 0机构: Schepens Eye Res Inst, Grousbeck Gene Therapy Ctr, Boston, MA USA