共 50 条
- [21] AAV-mediated gene therapy in dystrophin-Dp71 deficient mouse leads to blood-retinal barrier restorationGLIA, 2015, 63 : E193 - E193Vacca, O.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceEl Mathari, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceCharles-Messance, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceSene, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceBarbe, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceFouquet, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France论文数: 引用数: h-index:机构:Sahel, J. -A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France INSERM, CHNO Quinze Vingts, DHU ViewMaintain, DHOS CIC 1423, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France论文数: 引用数: h-index:机构:Dalkara, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, FranceRendon, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France INSERM, U968, Paris, France CNRS, UMR 7210, Paris, France Univ Paris 06, Sorbonne Univ, Inst Vis, UMR S 968, F-75475 Paris, France
- [22] Exosomal AAV-mediated SERCA2a Gene Transfer Improves Cardiac Function in a Mouse Model of Heart FailureCIRCULATION RESEARCH, 2019, 125Adamiak, Marta论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAJha, Divya论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USALiang Yaxuan论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAMathiyalagan, Prabhu论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAAgarwal, Neha论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAKohlbrenner, Erik论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAChepurko, Elena论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAJeong, Dongtak论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USACeholski, Delaine论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USADubois, Nicole论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med Mt Sinai, Black Family Stem Cell Inst, Mindich Child Hlth & Dev Inst, Dept Dev & Regenerat Biol, New York, NY 10029 USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USAHajjar, Roger论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USASahoo, Susmita论文数: 0 引用数: 0 h-index: 0机构: Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA Icahn Sch Med, Cardiovasc Rsch Cntr, New York, NY USA
- [23] AAV-mediated gene therapy in Dystrophin-Dp71 deficient mouse leads to blood-retinal barrier permeability restorationINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2014, 55 (13)Vacca, Ophelie论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceEl Mathari, Brahim论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceDarche, Marie论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceBarbe, Peggy论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceSchaffer, David V.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Dept Chem Engn, Dept Bioengn, Berkeley, CA 94720 USA Helen Wills Neurosci Inst, Berkeley, CA USA UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceFlannery, John Gerard论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Helen Wills Neurosci Inst, Berkeley, CA USA UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceSahel, Jose Alain论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France Fdn Ophtalmol Adolphe Rothschild, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France论文数: 引用数: h-index:机构:Dalkara, Deniz论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, FranceRendon, Alvaro论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France UPMC Univ Paris 06, INSERM, Inst Vis, CNRS,CHNO Quinze Vingts, Paris, France
- [24] Study on AAV-mediated gene therapy for diabetes in humanized liver mouse to predict efficacy in humansBIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 2016, 478 (03) : 1254 - 1260Hashimoto, Haruo论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanMizushima, Tomoko论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanOgura, Tomoyuki论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanKagawa, Takahiro论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanTomiyama, Kayo论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanTakahashi, Ri-ichi论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanYagoto, Mika论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanKawai, Kenji论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanChijiwa, Tsuyoshi论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanNakamura, Masato论文数: 0 引用数: 0 h-index: 0机构: Tokai Univ, Sch Med, Dept Pathol, 143 Shimokasuya, Isehara, Kanagawa 2591193, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, JapanSuemizu, Hiroshi论文数: 0 引用数: 0 h-index: 0机构: Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan Cent Inst Expt Anim, Kawasaki Ku, 3-25-12 Tonomachi, Kawasaki, Kanagawa 2100821, Japan
- [25] AAV-mediated gene therapy restores retinal function and vision in the RPGRIP1-deficient dogINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2013, 54 (15)Petit, Lolita论文数: 0 引用数: 0 h-index: 0机构: INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceLheriteau, Elsa论文数: 0 引用数: 0 h-index: 0机构: INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceWeber, Michel论文数: 0 引用数: 0 h-index: 0机构: CHU Hotel Dieu, Serv Opthalmol, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceLe Meur, Guylene论文数: 0 引用数: 0 h-index: 0机构: CHU Hotel Dieu, Serv Opthalmol, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceDeschamps, Jack-Yves论文数: 0 引用数: 0 h-index: 0机构: Nantes Atlantic Coll Vet Med Food Sci & Engn, ONIRIS, Emergency & Crit Care Unit, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceMoullier, Philippe论文数: 0 引用数: 0 h-index: 0机构: INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France Univ Florida, Coll Med, Dept Mol Genet & Microbiol, Gainesville, FL USA INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, FranceRolling, Fabienne论文数: 0 引用数: 0 h-index: 0机构: INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France INSERM, UMR 1089, Lab Therapie Genique, Inst Rech Therapeut 1, Nantes, France
- [26] AAV-mediated gene therapy to treat ocular failure in NCLs caused by transmembrane protein deficienciesHUMAN GENE THERAPY, 2018, 29 (12) : A169 - A169Holthaus, S. Kleine论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandAristorena, M.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandHoke, J.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandMaswood, R.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandSemenyuk, O.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandPearson, R. A.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandStorch, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Hamburg Eppendorf, Hamburg, Germany UCL, London, EnglandSmith, A. J.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandMole, S. E.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, EnglandAli, R. R.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England UCL, London, England
- [27] AAV-mediated follistatin gene therapy improves functional outcomes in the TIC-DUX4 mouse model of FSHDJCI INSIGHT, 2018, 3 (22):Giesige, Carlee R.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAWallace, Lindsay M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAHeller, Kristin N.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAEidahl, Jocelyn O.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USASaad, Nizar Y.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAFowler, Allison M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAPyne, Nettie K.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAAl-Kharsan, Mustafa论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USARashnonejad, Afrooz论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAChermahini, Gholamhossein Amini论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USADomire, Jacqueline S.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Oregon Hlth & Sci Univ, Portland, OR 97201 USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAMukweyi, Diana论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA West Ward Pharmaceut, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAGarwick-Coppens, Sara E.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAGuckes, Susan M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAMcLaughlin, K. John论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAMeyer, Kathrin论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USARodino-Klapac, Louise R.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USAHarper, Scott Q.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Ohio State Univ, Biomed Sci Grad Program, Columbus, OH 43210 USA
- [28] Therapeutic Efficacy of Bone Marrow Transplant, Intracranial AAV-mediated Gene Therapy, or Both in the Mouse Model of MPS IIIBMOLECULAR THERAPY, 2010, 18 (05) : 873 - 880Heldermon, Coy D.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USA Univ Florida, Dept Med, Gainesville, FL USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAOhlemiller, Kevin K.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Otolaryngol, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAHerzog, Erik D.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Biol, St Louis, MO 63130 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAVogler, Carole论文数: 0 引用数: 0 h-index: 0机构: St Louis Univ, Sch Med, Dept Pathol, St Louis, MO 63104 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAQin, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAWozniak, David F.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Psychiat, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USATan, Yun论文数: 0 引用数: 0 h-index: 0机构: St Louis Univ, Sch Med, Dept Surg, St Louis, MO USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USAOrrock, John L.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Biol, St Louis, MO 63130 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USASands, Mark S.论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Genet, St Louis, MO 63110 USA Washington Univ, Sch Med, Dept Internal Med, St Louis, MO 63110 USA
- [29] Stress-Induced Mouse Model of the Cardiac Manifestations of Friedreich's Ataxia Corrected by AAV-mediated Gene TherapyHUMAN GENE THERAPY, 2020, 31 (15-16) : 819 - 827Salami, Christiana O.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAJackson, Katie论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAJose, Clarisse论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAAlyass, Laith论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USACisse, Georges-Ibrahim论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USADe, Bishnu P.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAStiles, Katie M.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAChiuchiolo, Maria J.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USASondhi, Dolan论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USACrystal, Ronald G.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USAKaminsky, Stephen M.论文数: 0 引用数: 0 h-index: 0机构: Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA Weill Cornell Med Coll, Dept Med Genet, 1300 York Ave,Box 164, New York, NY 10065 USA
- [30] Life-long liver-specific AAV-mediated gene therapy in a Crigler-Najjar mouse modelHUMAN GENE THERAPY, 2013, 24 (12) : A133 - A133Bortolussi, G.论文数: 0 引用数: 0 h-index: 0机构: ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyZentilin, L.论文数: 0 引用数: 0 h-index: 0机构: ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyVanikova, J.论文数: 0 引用数: 0 h-index: 0机构: Charles Univ Prague, Inst Med Biochem & Lab Med, Fac Med 1, Prague, Czech Republic ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyVianello, E.论文数: 0 引用数: 0 h-index: 0机构: CSF, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyMancarella, A.论文数: 0 引用数: 0 h-index: 0机构: CSF, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyBockor, L.论文数: 0 引用数: 0 h-index: 0机构: ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyBellarosa, C.论文数: 0 引用数: 0 h-index: 0机构: CSF, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyTiribelli, C.论文数: 0 引用数: 0 h-index: 0机构: CSF, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyVitek, L.论文数: 0 引用数: 0 h-index: 0机构: Charles Univ Prague, Inst Med Biochem & Lab Med, Fac Med 1, Prague, Czech Republic ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyGiacca, M.论文数: 0 引用数: 0 h-index: 0机构: ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, ItalyMuro, A. F.论文数: 0 引用数: 0 h-index: 0机构: ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy ICGEB, Int Ctr Biotechnol & Genet Engn, Trieste, Italy