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- [41] Combined AAV-mediated gene replacement therapy improves auditory function in a mouse model of human DFNB42 deafnessMOLECULAR THERAPY, 2023, 31 (09) : 2783 - 2795Isgrig, Kevin论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USACartagena-Rivera, Alexander X.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Biomed Imaging & Bioengn, Sect Mechanobiol, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USAWang, Hong Jun论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USAGrati, Mhamed论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USAFernandez, Katharine A.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Sect Sensory Cell Biol, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USAFriedman, Thomas B.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Lab Mol Genet, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USABelyantseva, Inna A.论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Lab Mol Genet, NIH, Bethesda, MD USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USAChien, Wade论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USA Johns Hopkins Sch Med, Dept Otolaryngol Head & Neck Surg, Baltimore, MD USA 35A 1F220,35A Covent Dr, Bethesda, MD 20892 USA Natl Inst Deafness & Other Commun Disorders, Inner Ear Gene Therapy Program, NIH, Bethesda, MD USA
- [42] AAV-mediated Stambp gene replacement therapy rescues neurological defects in a mouse model of microcephaly-capillary malformation syndromeMOLECULAR THERAPY, 2024, 32 (11) : 4095 - 4107Hu, Meixin论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaLi, Jun论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Inst Pediat, Shanghai 200032, Peoples R China Fudan Univ, Inst Biomed Sci, Shanghai Key Lab Med Epigenet, Int Colab Med Epigenet & Metab,Minist Sci & Techno, Shanghai 200032, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaDeng, Jingxin论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaLiu, Chunxue论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaLiu, Yingying论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Inst Pediat, Shanghai 200032, Peoples R China Fudan Univ, Inst Biomed Sci, Shanghai Key Lab Med Epigenet, Int Colab Med Epigenet & Metab,Minist Sci & Techno, Shanghai 200032, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaLi, Huiping论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China Fudan Univ Xiamen, Xiamen Childrens Hosp, Childrens Hosp, Dept Child Hlth Care, Xiamen 361006, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaFeng, Weijun论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Inst Pediat, Shanghai 200032, Peoples R China Fudan Univ, Inst Biomed Sci, Shanghai Key Lab Med Epigenet, Int Colab Med Epigenet & Metab,Minist Sci & Techno, Shanghai 200032, Peoples R China Fudan Univ Xiamen, Xiamen Childrens Hosp, Fujian Key Lab Neonatal Dis, Xiamen Key Lab Neonatal Dis,Childrens Hosp, Xiamen 361006, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R ChinaXu, Xiu论文数: 0 引用数: 0 h-index: 0机构: Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China Fudan Univ, Childrens Hosp, Natl Childrens Med Ctr, Dept Child Hlth Care, Shanghai, Peoples R China
- [43] Optimization of hematopoietic stem cell transplantation to effect the recombinant AAV-mediated gene therapy of hemoglobinopathiesMOLECULAR BIOLOGY OF THE CELL, 2001, 12 : 522A - 522AOhi, S论文数: 0 引用数: 0 h-index: 0机构: Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USA Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USAJian, PS论文数: 0 引用数: 0 h-index: 0机构: Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USA Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USAAguilar, AA论文数: 0 引用数: 0 h-index: 0机构: Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USA Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USAKim, BC论文数: 0 引用数: 0 h-index: 0机构: Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USA Howard Univ, Ctr Sickle Cell Dis, Washington, DC 20059 USA
- [44] AAV-mediated in vivo CAR gene therapy for targeting human T-cell leukemiaBlood Cancer Journal, 11Waqas Nawaz论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolBilian Huang论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolShijie Xu论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolYanlei Li论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolLinjing Zhu论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolHu Yiqiao论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolZhiwei Wu论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical SchoolXilin Wu论文数: 0 引用数: 0 h-index: 0机构: Nanjing University,Center for Public Health Research, Medical School
- [45] AAV-mediated in vivo CAR gene therapy for targeting human T-cell leukemiaBLOOD CANCER JOURNAL, 2021, 11 (06)Nawaz, Waqas论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China Nanjing Univ, State Key Lab Analyt Chem Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Jiangsu Key Lab Mol Med, Nanjing, Peoples R China Nanjing Univ, Sch Med, State Key Lab Pharmaceut Biotechnol, Nanjing, Peoples R China Nanjing Univ, Sch Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaHuang, Bilian论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China Nanjing Univ, State Key Lab Analyt Chem Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Jiangsu Key Lab Mol Med, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaXu, Shijie论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China Nanjing Univ, State Key Lab Analyt Chem Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Jiangsu Key Lab Mol Med, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaLi, Yanlei论文数: 0 引用数: 0 h-index: 0机构: Y Clone Med Sci Co Ltd, Suzhou, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaZhu, Linjing论文数: 0 引用数: 0 h-index: 0机构: Abrev Biotechnol, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaYiqiao, Hu论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, State Key Lab Pharmaceut Biotechnol, Nanjing, Peoples R China Nanjing Univ, Sch Life Sci, Nanjing, Peoples R China Nanjing Univ, Inst Drug R&D, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaWu, Zhiwei论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China Nanjing Univ, State Key Lab Analyt Chem Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Jiangsu Key Lab Mol Med, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R ChinaWu, Xilin论文数: 0 引用数: 0 h-index: 0机构: Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China Nanjing Univ, State Key Lab Analyt Chem Life Sci, Nanjing, Peoples R China Nanjing Univ, Sch Med, Jiangsu Key Lab Mol Med, Nanjing, Peoples R China Nanjing Univ, Sch Med, Ctr Publ Hlth Res, Nanjing, Peoples R China
- [46] AAV-Mediated Progranulin Delivery to a Mouse Model of FTD/CNL Causes T Cell-Mediated ToxicityNEUROLOGY, 2019, 92 (15)Amado, Defne论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USARieders, Julianne论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Pathol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USADiatta, Fortunay论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USACon, Pilar Hernandez论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USASinger, Adina论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USAMak, Jordan论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USAZhang, Junxian论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USALancaster, Eric论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USADavidson, Beverly论文数: 0 引用数: 0 h-index: 0机构: Childrens Hosp Philadelphia, Pathol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USAChen-Plotkin, Alice论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Neurol, Philadelphia, PA 19104 USA Univ Penn, Neurol, Philadelphia, PA 19104 USA
- [47] AAV-Mediated Progranulin Delivery to a Mouse Model of Progranulin Deficiency Causes T Cell-Mediated ToxicityMOLECULAR THERAPY, 2019, 27 (02) : 465 - 478Amado, Defne A.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USARieders, Julianne M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, 3501 Civ Ctr Blvd,5060 CTRB, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USADiatta, Fortunay论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USAHernandez-Con, Pilar论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USASinger, Adina论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USAMak, Jordan T.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USAZhang, Junxian论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USALancaster, Eric论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USADavidson, Beverly L.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA Childrens Hosp Philadelphia, 3501 Civ Ctr Blvd,5060 CTRB, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USAChen-Plotkin, Alice S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA Univ Penn, Perelman Sch Med, Dept Neurol, 3 W Gates,3400 Spruce St, Philadelphia, PA 19104 USA
- [48] AAV-mediated base-editing therapy ameliorates the disease phenotypes in a mouse model of retinitis pigmentosaNATURE COMMUNICATIONS, 2023, 14 (01)Wu, Yidong论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R China Natl Clin Res Ctr Eye Dis, Shanghai, Peoples R China Shanghai Key Lab Ocular Fundus Dis, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaWan, Xiaoling论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R China Natl Clin Res Ctr Eye Dis, Shanghai, Peoples R China Shanghai Key Lab Ocular Fundus Dis, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaZhao, Dongdong论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaChen, Xuxu论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaWang, Yujie论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaTang, Xinxin论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaLi, Ju论文数: 0 引用数: 0 h-index: 0机构: Tianjin Normal Univ, Coll Life Sci, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaLi, Siwei论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaSun, Xiaodong论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R China Natl Clin Res Ctr Eye Dis, Shanghai, Peoples R China Shanghai Key Lab Ocular Fundus Dis, Shanghai, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaBi, Changhao论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R ChinaZhang, Xueli论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Tianjin Inst Ind Biotechnol, Tianjin, Peoples R China Natl Technol Innovat Ctr Synthet Biol, Tianjin, Peoples R China Shanghai Jiao Tong Univ, Shanghai Gen Hosp, Dept Ophthalmol, Sch Med, Shanghai, Peoples R China
- [49] AAV-mediated base-editing therapy ameliorates the disease phenotypes in a mouse model of retinitis pigmentosaNature Communications, 14Yidong Wu论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalXiaoling Wan论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalDongdong Zhao论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalXuxu Chen论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalYujie Wang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalXinxin Tang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalJu Li论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalSiwei Li论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalXiaodong Sun论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalChanghao Bi论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General HospitalXueli Zhang论文数: 0 引用数: 0 h-index: 0机构: Shanghai Jiao Tong University School of Medicine,Department of Ophthalmology, Shanghai General Hospital
- [50] Novel AAV-mediated genome editing therapy improves health and survival in a mouse model of methylmalonic acidemiaPLOS ONE, 2022, 17 (09):Zhang, Shengwen论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USABastille, Amy论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAGordo, Susana论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USARamesh, Nikhil论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAVora, Jenisha论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAMcCarthy, Elizabeth论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAZhang, Xiaohan论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAFrank, Dylan论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAKo, Chih-Wei论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAWu, Carmen论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAWalsh, Noel论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAAmarwani, Shreya论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USALiao, Jing论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAXiong, Qiang论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USADrouin, Lauren论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAHebben, Matthias论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAChiang, Kyle论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USAChau, B. Nelson论文数: 0 引用数: 0 h-index: 0机构: LogicBio Therapeut Inc, Lexington, MA 02421 USA LogicBio Therapeut Inc, Lexington, MA 02421 USA