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- [32] AAV-mediated gene replacement therapy in cell culture models of an inherited retinal degenerationIRISH JOURNAL OF MEDICAL SCIENCE, 2021, 190 (SUPPL 2) : 62 - 62Shortall, Ciara论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandLane, A.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandJovanovic, K.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandPalfi, A.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandChadderton, N.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandKenna, P. F.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Royal Victoria Eye & Ear Hosp, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandCarrigan, M.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandDockery, A.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandKeegan, D.论文数: 0 引用数: 0 h-index: 0机构: Mater Misericordiae Univ Hosp, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandO'Byrne, J.论文数: 0 引用数: 0 h-index: 0机构: Mater Misericordiae Univ Hosp, Dublin, Ireland Trinity Coll Dublin, Dublin, IrelandOttaviani, D.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandPanes, A.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandShen, S.论文数: 0 引用数: 0 h-index: 0机构: Natl Univ Ireland Galway, Galway, Ireland Trinity Coll Dublin, Dublin, IrelandHardcastle, A. J.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandCheetham, M. E.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Trinity Coll Dublin, Dublin, IrelandFarrar, G. J.论文数: 0 引用数: 0 h-index: 0机构: Trinity Coll Dublin, Dublin, Ireland Trinity Coll Dublin, Dublin, Ireland
- [33] Mitigation of cerebellar neuropathy in globoid cell leukodystrophy mice by AAV-mediated gene therapyGENE, 2015, 571 (01) : 81 - 90Lin, Dar-Shong论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Pediat, Taipei 10449, Taiwan Mackay Med Coll, Dept Med, New Taipei, Taiwan Natl Taipei Univ Technol, Dept Chem Engn & Biotechnol, Taipei 106, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, Taiwan论文数: 引用数: h-index:机构:Lee, Allan Yueh-Luen论文数: 0 引用数: 0 h-index: 0机构: Natl Hlth Res Inst, Natl Inst Canc Res, Miaoli, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanHo, Che-Sheng论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Pediat, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanLiu, Hsuan-Liang论文数: 0 引用数: 0 h-index: 0机构: Natl Taipei Univ Technol, Dept Chem Engn & Biotechnol, Taipei 106, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanWang, Tuen-Jen论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Lab Med, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanJian, Yuan-Ren论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Med Res, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanHsu, Jui-Cheng论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Med Res, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanHuang, Zon-Darr论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Med Res, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanLee, Tsung-Han论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Med Res, Taipei 10449, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, TaiwanChiang, Ming-Fu论文数: 0 引用数: 0 h-index: 0机构: Mackay Mem Hosp, Dept Neurosurg, Taipei 10449, Taiwan Taipei Med Univ, Inst Injury Prevent & Control, Taipei, Taiwan Mackay Mem Hosp, Dept Pediat, Taipei 10449, Taiwan
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- [35] AAV-mediated Gene Delivery in Dp71-null Mouse Model with Compromised BarriersGLIA, 2014, 62 (03) : 468 - 476Vacca, Ophelie论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceDarche, Marie论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceSchaffer, David V.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Dept Bioengn, Dept Chem Engn, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceFlannery, John G.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Berkeley, Dept Mol & Cell Biol, Helen Wills Neurosci Inst, Berkeley, CA 94720 USA Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceSahel, Jose-Alain论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France Fdn Ophtalmol Adolphe Rothschild, Paris, France UCL, Inst Ophthalmol, London WC1E 6BT, England Acad Sci Inst France, Paris, France Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceRendon, Alvaro论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, FranceDalkara, Deniz论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France Univ Paris 06, UPMC, INSERM, CNRS,CHNO Quinze Vingts,Inst Vis, Paris, France
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- [37] AAV-mediated gene therapy in Dystrophin-Dp71 deficient mouse leads to blood-retinal barrier restoration and oedema reabsorptionHUMAN MOLECULAR GENETICS, 2016, 25 (14) : 3070 - 3079Vacca, Ophelie论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France Univ Paris Sud, Neurosci Paris Saclay Inst NeuroPSI, CNRS UMR 9197, Cognit & Behav, F-91405 Orsay, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceCharles-Messance, Hugo论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceEl Mathari, Brahim论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceSene, Abdoulaye论文数: 0 引用数: 0 h-index: 0机构: Dept Ophthalmol, Therapeut, St Louis, MO 63103 USA UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceBarbe, Peggy论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceFouquet, Stephane论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceAragon, Jorge论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France IPN, CINVESTAV Res Ctr Adv Studies, Dept Genet & Mol Biol, Mexico City 07360, DF, Mexico UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceDarche, Marie论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceGiocanti-Auregan, Audrey论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France Avicenne Hosp, Dept Ophthalmol, F-93000 Bobigny, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France论文数: 引用数: h-index:机构:Sahel, Jose-Alain论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France DHOS CIC, INSERM, DHU Sight Restore, CHNO Quinze Vingts, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France论文数: 引用数: h-index:机构:Montanez, Cecilia论文数: 0 引用数: 0 h-index: 0机构: IPN, CINVESTAV Res Ctr Adv Studies, Dept Genet & Mol Biol, Mexico City 07360, DF, Mexico UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceDalkara, Deniz论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, FranceRendon, Alvaro论文数: 0 引用数: 0 h-index: 0机构: UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France UPMC Univ Paris 06, Sorbonne Univ, Inst Vis, INSERM,CNRS, F-75012 Paris, France
- [38] Reduction of retinal ganglion cell death in mouse models of familial dysautonomia using AAV-mediated gene therapy and splicing modulatorsScientific Reports, 13Anastasia Schultz论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyShun-Yun Cheng论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyEmily Kirchner论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyStephanann Costello论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyHeini Miettinen论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyMarta Chaverra论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyColin King论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyLynn George论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyXin Zhao论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyJana Narasimhan论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyMarla Weetall论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologySusan Slaugenhaupt论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyElisabetta Morini论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyClaudio Punzo论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell BiologyFrances Lefcort论文数: 0 引用数: 0 h-index: 0机构: Montana State University,Department of Microbiology and Cell Biology
- [39] Reduction of retinal ganglion cell death in mouse models of familial dysautonomia using AAV-mediated gene therapy and splicing modulatorsSCIENTIFIC REPORTS, 2023, 13 (01)Schultz, Anastasia论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USACheng, Shun-Yun论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Neurobiol & Gene Therapy Ctr, Dept Ophthalmol, Chan Med Sch, Worcester, MA USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAKirchner, Emily论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp Res Inst, Ctr Genom Med, Boston, MA USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USACostello, Stephanann论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAMiettinen, Heini论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAChaverra, Marta论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAKing, Colin论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAGeorge, Lynn论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ Billings, Dept Biol & Phys Sci, Billings, MT USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAZhao, Xin论文数: 0 引用数: 0 h-index: 0机构: PTC Therapeut Inc, South Plainfield, NJ 07080 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USANarasimhan, Jana论文数: 0 引用数: 0 h-index: 0机构: PTC Therapeut Inc, South Plainfield, NJ 07080 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAWeetall, Marla论文数: 0 引用数: 0 h-index: 0机构: PTC Therapeut Inc, South Plainfield, NJ 07080 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USASlaugenhaupt, Susan论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp Res Inst, Ctr Genom Med, Boston, MA USA Massachusetts Gen Hosp Res Inst, Dept Neurol, Boston, MA USA Harvard Med Sch, Boston, MA USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAMorini, Elisabetta论文数: 0 引用数: 0 h-index: 0机构: Massachusetts Gen Hosp Res Inst, Ctr Genom Med, Boston, MA USA Massachusetts Gen Hosp Res Inst, Dept Neurol, Boston, MA USA Harvard Med Sch, Boston, MA USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USAPunzo, Claudio论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Neurobiol & Gene Therapy Ctr, Dept Ophthalmol, Chan Med Sch, Worcester, MA USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USALefcort, Frances论文数: 0 引用数: 0 h-index: 0机构: Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA Montana State Univ, Dept Microbiol & Cell Biol, Bozeman, MT 59717 USA
- [40] AAV-Mediated Gene Therapy to Target the Progressive Neurodegeneration in a Mouse Model of Xeroderma Pigmentosum - Cockayne Syndrome (XP-CS)MOLECULAR THERAPY, 2023, 31 (04) : 349 - 349Daugherty, Audrey L.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USAChauhan, Monika论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USAKhadir, Fatemeh论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USAHoffman, Alexandra论文数: 0 引用数: 0 h-index: 0机构: Univ Maryland, Baltimore, MD USA Univ Minnesota, Dept Neurol, Minneapolis, MN USASuzuki-Hatano, Silveli论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USARizzo, Skylar A.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Med Scientist Training Program, Rochester, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USAVermeij, Wilbert P.论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Utrecht, Netherlands Oncode Inst, Utrecht, Netherlands Univ Minnesota, Dept Neurol, Minneapolis, MN USAHoeijmakers, Jan H. J.论文数: 0 引用数: 0 h-index: 0机构: Princess Maxima Ctr Pediat Oncol, Utrecht, Netherlands Oncode Inst, Utrecht, Netherlands Erasmus Univ, Dept Mol Genet, Med Ctr, Rotterdam, Netherlands Univ Minnesota, Dept Neurol, Minneapolis, MN USAKang, Peter B.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USAPacak, Christina A.论文数: 0 引用数: 0 h-index: 0机构: Univ Minnesota, Dept Neurol, Minneapolis, MN USA Univ Minnesota, Paul & Sheila Wellstone Muscular Dystrophy Ctr, Minneapolis, MN USA Univ Minnesota, Dept Neurol, Minneapolis, MN USA