CRISPR/Cas9-Based Gene Correction of Arginase-Deficient Human Induced Pluripotent Stem Cells to Recover Enzyme Function

被引：2
|
作者：
Brian Truong [1 ]
Lee, Patrick C. [1 ]
Vega-Crespo, Agustin [1 ]
Gilmore, William B. [2 ]
Hermann, Kip [2 ]
Kingman, Stephanie [2 ]
Tang, Jonathan K. [1 ]
Chang, Katherine M. [1 ]
Byrne, James A. [1 ]
Lipshutz, Gerald S. [2 ]
机构：
[1] Univ Calif Los Angeles, Mol & Med Pharmacol, Los Angeles, CA USA
[2] Univ Calif Los Angeles, Surg, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33156-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
347
引用
收藏
页码：S139 / S139
页数：1
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