CRISPR/Cas9-Based Gene Correction of Arginase-Deficient Human Induced Pluripotent Stem Cells to Recover Enzyme Function

被引：2
|
作者：
Brian Truong [1 ]
Lee, Patrick C. [1 ]
Vega-Crespo, Agustin [1 ]
Gilmore, William B. [2 ]
Hermann, Kip [2 ]
Kingman, Stephanie [2 ]
Tang, Jonathan K. [1 ]
Chang, Katherine M. [1 ]
Byrne, James A. [1 ]
Lipshutz, Gerald S. [2 ]
机构：
[1] Univ Calif Los Angeles, Mol & Med Pharmacol, Los Angeles, CA USA
[2] Univ Calif Los Angeles, Surg, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33156-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
347
引用
收藏
页码：S139 / S139
页数：1
相关论文
共 50 条
  • [31] The use of CRISPR/Cas9-based gene editing strategies to explore cancer gene function in mice
    van der Weyden, Louise
    Jonkers, Jos
    Adams, David J.
    CURRENT OPINION IN GENETICS & DEVELOPMENT, 2021, 66 : 57 - 62
  • [32] FACS-assisted CRISPR-Cas9 genome editing of human induced pluripotent stem cells
    Caillaud, Amandine
    Leveque, Antoine
    Thedrez, Aurelie
    Girardeau, Aurore
    Canac, Robin
    Bray, Lise
    Baudic, Manon
    Barc, Julien
    Gaborit, Nathalie
    Lamirault, Guillaume
    Gardie, Betty
    Idriss, Salam
    Rimbert, Antoine
    May, Cedric Le
    Cariou, Bertrand
    Si-Tayeb, Karim
    STAR PROTOCOLS, 2022, 3 (04):
  • [33] Correction of DMD Mutations in Human iPS-Derived Muscle Cells by Single-Cut CRISPR/Cas9-Based Gene Editing
    Al Tanoury, Ziad
    Rao, Lingjun
    Ahmed, Riffat
    Ai, Yulan
    Nixon, Ben
    Lee, Theodore
    Tsai, Phoebe
    Caycedo, Cristina Rodriguez
    Min, Yi-Li
    Olson, Eric
    McVie-Wylie, Alison
    Fulga, Tudor
    MOLECULAR THERAPY, 2021, 29 (04) : 10 - 10
  • [34] CRISPR/Cas9-based GLA knockout to generate the female Fabry disease human induced pluripotent stem cell line MHHi001-A-15
    Juchem, Malte
    Lehmann, Nele
    Behrens, Yvonne Lisa
    Bar, Christian
    Thum, Thomas
    Hoepfner, Jeannine
    STEM CELL RESEARCH, 2024, 79
  • [35] An episomal vector-based CRISPR/Cas9 system for highly efficient gene knockout in human pluripotent stem cells
    Yifang Xie
    Daqi Wang
    Feng Lan
    Gang Wei
    Ting Ni
    Renjie Chai
    Dong Liu
    Shijun Hu
    Mingqing Li
    Dajin Li
    Hongyan Wang
    Yongming Wang
    Scientific Reports, 7
  • [36] An episomal vector-based CRISPR/Cas9 system for highly efficient gene knockout in human pluripotent stem cells
    Xie, Yifang
    Wang, Daqi
    Lan, Feng
    Wei, Gang
    Ni, Ting
    Chai, Renjie
    Liu, Dong
    Hu, Shijun
    Li, Mingqing
    Li, Dajin
    Wang, Hongyan
    Wang, Yongming
    SCIENTIFIC REPORTS, 2017, 7
  • [37] CRISPR/Cas9 induced deletion for the correction of the human dystrophin gene
    Duchene, B.
    Iyombe-Engembe, J-P
    Lo, M.
    Reichelt, P.
    Rousseau, J.
    Ouellet, D. L.
    Tremblay, J. P.
    HUMAN GENE THERAPY, 2017, 28 (12) : A54 - A54
  • [38] Utilizing CRISPR-CAS9 Gene Editing Technology in Human Pluripotent Stem Cells to Study Platelet Integrin αIIbβ3 Function
    Fong, Karen
    Jobaliya, Chintan
    Maguire, Jean Ann
    Poncz, Mortimer
    French, Deborah L.
    Bennett, Joel S.
    BLOOD, 2020, 136
  • [39] Reversal of Phenotypic Abnormalities by CRISPR/Cas9-Mediated Gene Correction in Huntington Disease Patient-Derived Induced Pluripotent Stem Cells
    Xu, Xiaohong
    Tay, Yilin
    Sim, Bernice
    Yoon, Su-In
    Huang, Yihui
    Ooi, Jolene
    Utami, Kagistia Hana
    Ziaei, Amin
    Ng, Bryan
    Radulescu, Carola
    Low, Donovan
    Ng, Alvin Yu Jin
    Loh, Marie
    Venkatesh, Byrappa
    Ginhoux, Florent
    Augustine, George J.
    Pouladi, Mahmoud A.
    STEM CELL REPORTS, 2017, 8 (03): : 619 - 633
  • [40] Generation and Characterization of CPVT1 Cardiomyocytes using Human Induced Pluripotent Stem Cells and CRISPR/Cas9 Gene Editing
    Yamaguchi, Naohiro
    Zhang, Xiao-Hua
    Wei, Hua
    Morad, Martin
    BIOPHYSICAL JOURNAL, 2018, 114 (03) : 116A - 116A
12345