CRISPR/Cas9-Based Gene Correction of Arginase-Deficient Human Induced Pluripotent Stem Cells to Recover Enzyme Function

被引：2
|
作者：
Brian Truong [1 ]
Lee, Patrick C. [1 ]
Vega-Crespo, Agustin [1 ]
Gilmore, William B. [2 ]
Hermann, Kip [2 ]
Kingman, Stephanie [2 ]
Tang, Jonathan K. [1 ]
Chang, Katherine M. [1 ]
Byrne, James A. [1 ]
Lipshutz, Gerald S. [2 ]
机构：
[1] Univ Calif Los Angeles, Mol & Med Pharmacol, Los Angeles, CA USA
[2] Univ Calif Los Angeles, Surg, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33156-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
347
引用
收藏
页码：S139 / S139
页数：1
相关论文
共 50 条
  • [21] Author Correction: An episomal vector-based CRISPR/Cas9 system for highly efficient gene knockout in human pluripotent stem cells
    Yifang Xie
    Daqi Wang
    Feng Lan
    Gang Wei
    Ting Ni
    Renjie Chai
    Dong Liu
    Shijun Hu
    Mingqing Li
    Dajin Li
    Hongyan Wang
    Yongming Wang
    Scientific Reports, 8
  • [22] Application of CRISPR/Cas9 to human-induced pluripotent stem cells: from gene editing to drug discovery
    Claudia De Masi
    Paola Spitalieri
    Michela Murdocca
    Giuseppe Novelli
    Federica Sangiuolo
    Human Genomics, 14
  • [23] Precision Genome Engineering in Human Induced Pluripotent Stem Cells Using CRISPR/CAS9
    Connelly, Jon P.
    Neilson, Amber M.
    Peters, Sam T.
    Martinez, Rita
    Milbrandt, Jeffrey D.
    Miller, Shondra M.
    MOLECULAR THERAPY, 2015, 23 : S262 - S262
  • [24] Endogenous Protein Tagging in Human Induced Pluripotent Stem Cells Using CRISPR/Cas9
    Haupt, Amanda
    Grancharova, Tanya
    Arakaki, Joy
    Fuqua, Margaret A.
    Roberts, Brock
    Gunawardane, Ruwanthi N.
    JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, 2018, (138):
  • [25] Application of CRISPR/Cas9 to human-induced pluripotent stem cells: from gene editing to drug discovery
    De Masi, Claudia
    Spitalieri, Paola
    Murdocca, Michela
    Novelli, Giuseppe
    Sangiuolo, Federica
    HUMAN GENOMICS, 2020, 14 (01)
  • [26] Reporter gene imaging “visualized” the integration of two growing technologies: CRISPR/Cas9-based genome editing and induced pluripotent stem cell therapy
    Arturo Chiti
    European Journal of Nuclear Medicine and Molecular Imaging, 2021, 48 : 664 - 665
  • [27] Genetic Correction of Duchenne Muscular Dystrophy by Multiplex CRISPR/Cas9-Based Gene Editing
    Ousterout, David G.
    Kabadi, Ami M.
    Thakore, Pratiksha I.
    Gersbach, Charles A.
    MOLECULAR THERAPY, 2014, 22 : S196 - S197
  • [28] CRISPR/Cas9-Based Functional Genomics in Human Induced Pluripotent Stem Cell-Derived Models: Can "the Stars Align" for Neurodegenerative Diseases?
    Chen, Yu
    Jong, Tiffany Ting-Yu
    Chen, Chase
    Sidransky, Ellen
    MOVEMENT DISORDERS, 2022, 37 (05) : 886 - 890
  • [29] Genome Editing in Induced Pluripotent Stem Cells using CRISPR/Cas9
    Ben Jehuda, Ronen
    Shemer, Yuval
    Binah, Ofer
    STEM CELL REVIEWS AND REPORTS, 2018, 14 (03) : 323 - 336
  • [30] Genome Editing in Induced Pluripotent Stem Cells using CRISPR/Cas9
    Ronen Ben Jehuda
    Yuval Shemer
    Ofer Binah
    Stem Cell Reviews and Reports, 2018, 14 : 323 - 336
12345