CRISPR/Cas9-Based Gene Correction of Arginase-Deficient Human Induced Pluripotent Stem Cells to Recover Enzyme Function

被引：2
|
作者：
Brian Truong [1 ]
Lee, Patrick C. [1 ]
Vega-Crespo, Agustin [1 ]
Gilmore, William B. [2 ]
Hermann, Kip [2 ]
Kingman, Stephanie [2 ]
Tang, Jonathan K. [1 ]
Chang, Katherine M. [1 ]
Byrne, James A. [1 ]
Lipshutz, Gerald S. [2 ]
机构：
[1] Univ Calif Los Angeles, Mol & Med Pharmacol, Los Angeles, CA USA
[2] Univ Calif Los Angeles, Surg, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2016年 / 24卷
关键词：
D O I：
10.1016/S1525-0016(16)33156-2
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
347
引用
收藏
页码：S139 / S139
页数：1
相关论文
共 50 条
  • [1] Restoring Ureagenesis in Hepatocytes by CRISPR/Cas9-mediated Genomic Addition to Arginase-deficient Induced Pluripotent Stem Cells
    Lee, Patrick C.
    Truong, Brian
    Vega-Crespo, Agustin
    Gilmore, W. Blake
    Hermann, Kip
    Angarita, Stephanie A. K.
    Tang, Jonathan K.
    Chang, Katherine M.
    Wininger, Austin E.
    Lam, Alex K.
    Schoenberg, Benjamen E.
    Cederbaum, Stephen D.
    Pyle, April D.
    Byrne, James A.
    Lipshutz, Gerald S.
    MOLECULAR THERAPY-NUCLEIC ACIDS, 2016, 5 : e394
  • [2] Automated CRISPR/Cas9-based genome editing of human pluripotent stem cells using the StemCellFactory
    Niessing, Bastian
    Breitkreuz, Yannik
    Elanzew, Andreas
    de Toledo, Marcelo A. S.
    Vajs, Peter
    Nolden, Marina
    Erkens, Frederik
    Wanek, Paul
    Yeung, Si Wah Christina Au
    Haupt, Simone
    Koenig, Niels
    Peitz, Michael
    Schmitt, Robert H.
    Zenke, Martin
    Bruestle, Oliver
    FRONTIERS IN BIOENGINEERING AND BIOTECHNOLOGY, 2024, 12
  • [3] Distinct genetic impact of CRISPR/Cas9 gene correction in human embryos compared to induced pluripotent stem cells
    Bekaert, B.
    Boel, A.
    De Witte, L.
    Cosemans, G.
    Tordeurs, L.
    De Loore, A. M.
    Lopes, S. M. Chuva de Sousa
    De Sutter, P.
    Stoop, D.
    Coucke, P.
    Menten, B.
    Heindryckx, B.
    HUMAN REPRODUCTION, 2022, 37
  • [4] Optimization of a CRISPR/Cas9-based strategy for the correction of CD40LG gene in human haematopoietic stem cells and T cells
    Vavassori, V.
    Mercuri, E.
    Schiroli, G.
    Marcovecchio, G.
    Albano, L.
    Castiello, M. C.
    Annoni, A.
    Capo, V.
    Margulies, C.
    Buquicchio, F.
    Cotta-Ramusino, C.
    Villa, A.
    Naldini, L.
    Genovese, P.
    HUMAN GENE THERAPY, 2018, 29 (12) : A102 - A102
  • [5] CRISPR/Cas9 gene correction of HbH-CS thalassemia-induced pluripotent stem cells
    Xie Yingjun
    Xie Yuhuan
    Chen Yuchang
    Li Dongzhi
    Wang Ding
    Song Bing
    Yang Yi
    Lu Dian
    Xue Yanting
    Xiong Zeyu
    Liu Nengqing
    Chen Diyu
    Sun Xiaofang
    Annals of Hematology, 2019, 98 : 2661 - 2671
  • [6] CRISPR/Cas9 gene correction of HbH-CS thalassemia-induced pluripotent stem cells
    Xie Yingjun
    Xie Yuhuan
    Chen Yuchang
    Li Dongzhi
    Wang Ding
    Song Bin
    Yang Yi
    Lu Dian
    Xue Yanting
    Xiong Zeyu
    Liu Nengqing
    Chen Diyu
    Sun Xiaofang
    ANNALS OF HEMATOLOGY, 2019, 98 (12) : 2661 - 2671
  • [7] Gene editing and clonal isolation of human induced pluripotent stem cells using CRISPR/Cas9
    Yumlu, Saniye
    Stumm, Juergen
    Bashir, Sanum
    Dreyer, Anne-Kathrin
    Lisowski, Pawel
    Danner, Eric
    Kuehn, Ralf
    METHODS, 2017, 121 : 29 - 44
  • [8] CRISPR-Cas Gene Perturbation and Editing in Human Induced Pluripotent Stem Cells
    van Essen, Max
    Riepsaame, Joey
    Jacob, John
    CRISPR JOURNAL, 2021, 4 (05): : 634 - 655
  • [9] CRISPR-Cas9: a promising tool for gene editing on induced pluripotent stem cells
    Kim, Eun Ji
    Kang, Ki Ho
    Ju, Ji Hyeon
    KOREAN JOURNAL OF INTERNAL MEDICINE, 2017, 32 (01): : 42 - 61
  • [10] Trichostatin A for Efficient CRISPR-Cas9 Gene Editing of Human Pluripotent Stem Cells
    Molugu, Kaivalya
    Khajanchi, Namita
    Lazzarotto, Cicera R.
    Tsai, Shengdar Q.
    Saha, Krishanu
    CRISPR JOURNAL, 2023, 6 (05): : 473 - 485
12345