Duchenne-Muscular Dystrophy: Long-Term efficacy of Steroid Treatment

被引：0
|
作者：
Manych, Matthias
机构：
来源：
FORTSCHRITTE DER NEUROLOGIE PSYCHIATRIE | 2018年 / 86卷 / 05期
关键词：
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
引用
收藏
页码：264 / 264
页数：1
相关论文
共 50 条
  • [41] Intermittent, low dosage prednisolone in the long term treatment of early Duchenne muscular dystrophy
    Dubowitz, V
    Kinali, M
    Mercuri, E
    Main, M
    Muntoni, F
    [J]. JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, 2003, 74 (08): : 1182 - 1182
  • [42] Long-Term Characterization of In Vivo Genome Editing in a Mouse Model of Duchenne Muscular Dystrophy
    Nelson, Christopher
    Gemberling, Matthew
    Madhavan, Sarina
    Rivera, Ruth M. Castellanos
    Asokan, Aravind
    Gersbach, Charles A.
    [J]. MOLECULAR THERAPY, 2017, 25 (05) : 100 - 101
  • [43] Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
    Caroline Le Guiner
    Laurent Servais
    Marie Montus
    Thibaut Larcher
    Bodvaël Fraysse
    Sophie Moullec
    Marine Allais
    Virginie François
    Maeva Dutilleul
    Alberto Malerba
    Taeyoung Koo
    Jean-Laurent Thibaut
    Béatrice Matot
    Marie Devaux
    Johanne Le Duff
    Jack-Yves Deschamps
    Inès Barthelemy
    Stéphane Blot
    Isabelle Testault
    Karim Wahbi
    Stéphane Ederhy
    Samia Martin
    Philippe Veron
    Christophe Georger
    Takis Athanasopoulos
    Carole Masurier
    Federico Mingozzi
    Pierre Carlier
    Bernard Gjata
    Jean-Yves Hogrel
    Oumeya Adjali
    Fulvio Mavilio
    Thomas Voit
    Philippe Moullier
    George Dickson
    [J]. Nature Communications, 8
  • [44] Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
    Le Guiner, Caroline
    Servais, Laurent
    Montus, Marie
    Larcher, Thibaut
    Fraysse, Bodvael
    Moullec, Sophie
    Allais, Marine
    Francois, Virginie
    Dutilleul, Maeva
    Malerba, Alberto
    Koo, Taeyoung
    Thibaut, Jean-Laurent
    Matot, Beatrice
    Devaux, Marie
    Le Duff, Johanne
    Deschamps, Jack-Yves
    Barthelemy, Ines
    Blot, Stephane
    Testault, Isabelle
    Wahbi, Karim
    Ederhy, Stephane
    Martin, Samia
    Veron, Philippe
    Georger, Christophe
    Athanasopoulos, Takis
    Masurier, Carole
    Mingozzi, Federico
    Carlier, Pierre
    Gjata, Bernard
    Hogrel, Jean-Yves
    Adjali, Oumeya
    Mavilio, Fulvio
    Voit, Thomas
    Moullier, Philippe
    Dickson, George
    [J]. NATURE COMMUNICATIONS, 2017, 8
  • [45] Long-term follow-up of dysphagia in adult patients with Duchenne muscular dystrophy
    Yamada, Yuka
    Kawakami, Michiyuki
    Wada, Ayako
    Fukui, Shogo
    Haruyama, Koshiro
    Otsuka, Tomoyoshi
    Liu, Meigen
    [J]. EUROPEAN JOURNAL OF PAEDIATRIC NEUROLOGY, 2018, 22 (05) : 786 - 790
  • [46] Long-Term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy
    Nelson, Christopher
    Wu, Yaoying
    Gemberling, Matthew
    Oliver, Matthew
    Bohning, Joel D.
    Robinson-Hamm, Jacqueline N.
    Bulaklak, Karen
    Rivera, Ruth M. Castellanos
    Collier, Joel H.
    Asokan, Aravind
    Gersbach, Charles A.
    [J]. MOLECULAR THERAPY, 2019, 27 (04) : 46 - 47
  • [47] Cataract development associated with long-term glucocorticoid therapy in Duchenne muscular dystrophy patients
    Rice, Melissa L.
    Wong, Brenda
    Horn, Paul S.
    Yang, Michael B.
    [J]. JOURNAL OF AAPOS, 2018, 22 (03): : 192 - 196
  • [48] Bone health in boys with Duchenne Muscular Dystrophy on long-term daily deflazacort therapy
    Mayo, A. L.
    Craven, B. C.
    McAdam, L. C.
    Biggar, W. D.
    [J]. NEUROMUSCULAR DISORDERS, 2012, 22 (12) : 1040 - 1045
  • [49] Long-term data with idebenone on respiratory function outcomes in patients with Duchenne muscular dystrophy
    Servais, Laurent
    Straathof, Chiara S. M.
    Schara, Ulrike
    Klein, Andrea
    Leinonen, Mika
    Hasham, Shabir
    Meier, Thomas
    De Waele, Liesbeth
    Gordish-Dressman, Heather
    McDonald, Craig M.
    Mayer, Oscar H.
    Voit, Thomas
    Mercuri, Eugenio
    Buyse, Gunnar M.
    [J]. NEUROMUSCULAR DISORDERS, 2020, 30 (01) : 5 - 16
  • [50] Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy
    Nelson, Christopher E.
    Wu, Yaoying
    Gemberling, Matthew P.
    Oliver, Matthew L.
    Waller, Matthew A.
    Bohning, Joel D.
    Robinson-Hamm, Jacqueline N.
    Bulaklak, Karen
    Rivera, Ruth M. Castellanos
    Collier, Joel H.
    Asokan, Aravind
    Gersbach, Charles A.
    [J]. NATURE MEDICINE, 2019, 25 (03) : 427 - +
12345