Expanding CRISPR Genome Editing Strategies in Hematopoietic Stem and Progenitor Cells for the Treatment of Hematologic Diseases

被引:0
|
作者
deDreuzy, Edouard
Chalishazar, Aditi
Heath, Jack
Margulies, Carrie M.
Labella, John
Viswanathan, Ramya
Loveluck, Katherine
Chang, KaiHsin
Jayaram, Hariharan
Zuris, John A.
Myer, Vic E.
Albright, Charlie
Cotta-Ramusino, Cecilia
Gori, Jennifer L.
机构
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
4619
引用
收藏
页数:2
相关论文
共 50 条
  • [11] A Versatile Tool for the Quantification of CRISPR/Cas9-Induced Genome Editing Events in Human Hematopoietic Cell Lines and Hematopoietic Stem/Progenitor Cells
    Jayavaradhan, Rajeswari
    Pillis, Devin M.
    Malik, Punam
    JOURNAL OF MOLECULAR BIOLOGY, 2019, 431 (01) : 102 - 110
  • [12] Highly Efficient Genome Editing of Murine and Human Hematopoietic Progenitor Cells by CRISPR/Cas9
    Gundry, Michael C.
    Brunetti, Lorenzo
    Lin, Angelique
    Mayle, Allison E.
    Kitano, Ayumi
    Wagner, Dimitrios
    Hsu, Joanne I.
    Hoegenauer, Kevin A.
    Rooney, Cliona M.
    Goodell, Margaret A.
    Nakada, Daisuke
    CELL REPORTS, 2016, 17 (05): : 1453 - 1461
  • [13] Ultra-deep sequencing validates safety of CRISPR/Cas9 genome editing in human hematopoietic stem and progenitor cells
    M. Kyle Cromer
    Valentin V. Barsan
    Erich Jaeger
    Mengchi Wang
    Jessica P. Hampton
    Feng Chen
    Drew Kennedy
    Jenny Xiao
    Irina Khrebtukova
    Ana Granat
    Tiffany Truong
    Matthew H. Porteus
    Nature Communications, 13
  • [14] Ultra-deep sequencing validates safety of CRISPR/Cas9 genome editing in human hematopoietic stem and progenitor cells
    Cromer, M. Kyle
    Barsan, Valentin V.
    Jaeger, Erich
    Wang, Mengchi
    Hampton, Jessica P.
    Chen, Feng
    Kennedy, Drew
    Xiao, Jenny
    Khrebtukova, Irina
    Granat, Ana
    Truong, Tiffany
    Porteus, Matthew H.
    NATURE COMMUNICATIONS, 2022, 13 (01)
  • [15] To CRISPR and beyond: the evolution of genome editing in stem cells
    Chen, Kuang-Yui
    Knoepfler, Paul S.
    REGENERATIVE MEDICINE, 2016, 11 (08) : 801 - 816
  • [16] Multiplexing CRISPR-Cas9 Genome Editing in Human Hematopoietic Stem and Effector Cells
    Dever, Daniel P.
    Bak, Rasmus O.
    Reinisch, Andreas
    Cruz, David
    Majeti, Ravindra
    Porteus, Matthew
    MOLECULAR THERAPY, 2017, 25 (05) : 343 - 343
  • [17] CRISPR genome editing in stem cells turns to gold
    Aravind Asokan
    Nature Materials, 2019, 18 : 1038 - 1039
  • [18] The Rise of CRISPR/Cas for Genome Editing in Stem Cells
    Shui, Bing
    Matias, Liz Hernandez
    Guo, Yi
    Peng, Ying
    STEM CELLS INTERNATIONAL, 2016, 2016
  • [19] CRISPR genome editing in stem cells turns to gold
    Asokan, Aravind
    NATURE MATERIALS, 2019, 18 (10) : 1038 - 1039
  • [20] AUTOMATED GMP-COMPATIBLE CRISPR-CAS9 EDITING OF HEMATOPOIETIC STEM AND PROGENITOR CELLS (HSPCS) FOR THE TREATMENT OF β-HEMOGLOBINOPATHIES
    Urena-Bailen, G.
    Block, M.
    CYTOTHERAPY, 2023, 25 (06) : S124 - S124