共 50 条
- [1] Automated GMP-compatible CRISPR-Cas9 editing of hematopoietic stem and progenitor cells (HSPCs) for the treatment of β-hemoglobinopathiesHUMAN GENE THERAPY, 2024, 35 (3-4) : A179 - A180Block, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Tubingen, Germany Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyUrena-Bailen, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Freiburg, Freiburg, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyGrandi, T.论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyAivazidou, F.论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyQuednau, J.论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyKrenz, D.论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyDaniel-Moreno, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Tubingen, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyLamsfus-Calle, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Tubingen, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyEpting, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Freiburg, Freiburg, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyHandgretinger, R.论文数: 0 引用数: 0 h-index: 0机构: Abu Dhabi Stem Cells Ctr, Abu Dhabi, U Arab Emirates Univ Childrens Hosp Tubingen, Tubingen, GermanyWild, S.论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Biotec, Cologne, Germany Univ Childrens Hosp Tubingen, Tubingen, GermanyMezger, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp Tubingen, Tubingen, Germany Univ Childrens Hosp Tubingen, Tubingen, Germany
- [2] Automated Good Manufacturing Practice-Compatible CRISPR-Cas9 Editing of Hematopoietic Stem and Progenitor Cells for Clinical Treatment of β-HemoglobinopathiesCRISPR JOURNAL, 2023, 6 (01): : 5 - 16Urena-Bailen, Guillermo论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyBlock, Milena论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyGrandi, Tommaso论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyAivazidou, Faidra论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyQuednau, Jona论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyKrenz, Dariusz论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyDaniel-Moreno, Alberto论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyLamsfus-Calle, Andres论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyEpting, Thomas论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp, Inst Clin Chem & Lab Med, Freiburg, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyHandgretinger, Rupert论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany Abu Dhabi Stem Cells Ctr, Abu Dhabi, U Arab Emirates Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyWild, Stefan论文数: 0 引用数: 0 h-index: 0机构: Miltenyi Botec BV & Co KG, Bergisch Gladbach, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, GermanyMezger, Markus论文数: 0 引用数: 0 h-index: 0机构: Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany Univ Childrens Hosp, Dept Gen Pediat Oncol & Hematol, Hoppe Seyler Str 1, DE-72076 Tubingen, Germany
- [3] Efficient GMP-compatible CRISPR-Cas mediated genome editing in hematopoietic stem and progenitor cellsTRANSFUSION MEDICINE AND HEMOTHERAPY, 2017, 44 : 81 - 81Turchiano, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Ctr Chron Immunodeficiency, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, GermanyHaas, S.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Ctr Chron Immunodeficiency, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, GermanyHildenbeutel, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Ctr Chron Immunodeficiency, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, GermanyPennucci, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Ctr Chron Immunodeficiency, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, GermanyCornu, T. I.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Ctr Chron Immunodeficiency, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, GermanyCathomen, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany Univ Freiburg, Inst Transfus Med & Gene Therapy, Med Ctr, Freiburg, Germany
- [4] Efficient GMP-compatible CRISPR/Cas mediated genome editing in haematopoietic stem and progenitor cellsHUMAN GENE THERAPY, 2017, 28 (12) : A55 - A55Turchiano, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, GermanyHaas, S. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, GermanyHildenbeutel, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, GermanyPennucci, V.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, GermanyCornu, T. I.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, GermanyCathomen, T.论文数: 0 引用数: 0 h-index: 0机构: Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany Univ Freiburg, Med Ctr, Ctr Chron Immunodeficiency, Freiburg, Germany Univ Freiburg, Med Ctr, Inst Transfus Med & Gene Therapy, Freiburg, Germany
- [5] Efficient gene editing in hematopoietic stem/progenitor cells with the CRISPR-Cas9 systemHUMAN GENE THERAPY, 2015, 26 (10) : A49 - A49Gori, J. L.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USAHeath, J. M.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USACollins, M. A.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USAFang, J. W.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USAFriedland, A. E.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USAWelstead, G. G.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USABumcrot, D.论文数: 0 引用数: 0 h-index: 0机构: Editas Med, Cambridge, MA USA Editas Med, Cambridge, MA USA
- [6] CRISPR-Cas9 Genome Editing of γ-Globin Promoters in Human Hematopoietic Stem Cells to Induce Erythrocyte Fetal Hemoglobin for Treatment of β-HemoglobinopathiesBLOOD, 2019, 134Metais, Jean-Yves论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USADoerfler, Phillip A.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAMayuranathan, Thiyagaraj论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USABauer, Daniel E.论文数: 0 引用数: 0 h-index: 0机构: Dana Farber, Canc & Blood Disorders Ctr, Cambridge, MA USA Dana Farber Canc Inst, Boston Childrens Hosp, Cambridge, MA USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAFowler, Stephanie论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAHsieh, Matthew论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Cellular & Mol Therapeut Branch, NIH, Bldg 10, Bethesda, MD 20892 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAKatta, Varun论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAKeriwala, Sagar论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USALazzarotto, Cicera论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USALuk, Kevin论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Dept Mol Cell & Canc Biol, Worcester, MA USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USANeel, Michael论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAPerry, Scott论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAPorter, Shaina论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USARyu, Byoung Y.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USASharma, Akshay论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAShea, Devlin论文数: 0 引用数: 0 h-index: 0机构: Boston Childrens Hosp, Boston, MA USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAPeters, Samuel论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USATisdale, John F.论文数: 0 引用数: 0 h-index: 0机构: NHLBI, Cellular & Mol Therapeut Branch, NIH, Bldg 10, Bethesda, MD 20892 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAWolfe, Scot A.论文数: 0 引用数: 0 h-index: 0机构: Umass Med Sch, Worcester, MA USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAWoodard, Kaitly Jensen论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAUchida, Naoya论文数: 0 引用数: 0 h-index: 0机构: NHLBI, CMTB, NIDDK, NIH,MCHB, Bldg 10, Bethesda, MD 20892 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAWu, Yuxuan论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAYao, Yu论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAZeng, Jing论文数: 0 引用数: 0 h-index: 0机构: Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAPruett-Miller, Shondra M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Ctr Adv Genome Engn CAGE, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USATsai, Shengdar Q.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USAWeiss, Mitchell J.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Hematol, 332 N Lauderdale St, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, 332 N Lauderdale St, Memphis, TN 38105 USA
- [7] Multiplexing CRISPR-Cas9 Genome Editing in Human Hematopoietic Stem and Effector CellsMOLECULAR THERAPY, 2017, 25 (05) : 343 - 343Dever, Daniel P.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Pediat, Palo Alto, CA 94304 USA Stanford Univ, Pediat, Palo Alto, CA 94304 USABak, Rasmus O.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Pediat, Palo Alto, CA 94304 USA Stanford Univ, Pediat, Palo Alto, CA 94304 USAReinisch, Andreas论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Div Hematol, Med, Palo Alto, CA 94304 USA Stanford Univ, Pediat, Palo Alto, CA 94304 USACruz, David论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Div Hematol, Med, Palo Alto, CA 94304 USA Stanford Univ, Pediat, Palo Alto, CA 94304 USA论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:
- [8] CRISPR-Cas9 Edited Hematopoietic Stem and Progenitor Cells for Friedreich's AtaxiaMOLECULAR THERAPY, 2022, 30 (04) : 135 - 135Sivakumar, Anusha论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USARainaldi, Joseph N.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USAWan, Rita论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USARocca, Celine J.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USACherqui, Stephanie论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA Univ Calif San Diego, Dept Pediat, San Diego, CA 92103 USA
- [9] Gene Editing with Crispr-Cas9 for Treating Beta-HemoglobinopathiesBLOOD, 2015, 126 (23)论文数: 引用数: h-index:机构:Bao, Gang论文数: 0 引用数: 0 h-index: 0机构: Rice Univ, Houston, TX USA Rice Univ, Houston, TX USAPorteus, Matthew H.论文数: 0 引用数: 0 h-index: 0机构: Stanford Univ, Dept Pediat, Sch Med, Canc Biol, Stanford, CA 94305 USA Rice Univ, Houston, TX USACornu, Tatjana论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Freiburg, Freiburg, Germany Rice Univ, Houston, TX USAMiccio, Annarita论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Imagine Inst, Paris, France Rice Univ, Houston, TX USACradick, Thomas论文数: 0 引用数: 0 h-index: 0机构: CRISPR Therapeut, Boston, MA USA Rice Univ, Houston, TX USACathomen, Toni论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr Freiburg, Freiburg, Germany Rice Univ, Houston, TX USALundberg, Ante论文数: 0 引用数: 0 h-index: 0机构: CRISPR THERAPEUT, Cambrdige, MA USA Rice Univ, Houston, TX USAMavilio, Fulvio论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Rice Univ, Houston, TX USA
- [10] Therapeutic gene editing strategies using CRISPR-Cas9 for the β-hemoglobinopathiesJOURNAL OF BIOMEDICAL RESEARCH, 2021, 35 (02): : 115 - 134Papizan, James B.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Ctr Adv Genome Engn, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USAPorter, Shaina N.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Ctr Adv Genome Engn, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USASharma, Akshay论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Bone Marrow Transplantat & Cellular Therapy, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USAPruett-Miller, Shondra M.论文数: 0 引用数: 0 h-index: 0机构: St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Ctr Adv Genome Engn, Memphis, TN 38105 USA St Jude Childrens Res Hosp, Dept Cellular & Mol Biol, 262 Danny Thomas Pl, Memphis, TN 38105 USA