Expanding CRISPR Genome Editing Strategies in Hematopoietic Stem and Progenitor Cells for the Treatment of Hematologic Diseases

被引：0
|
作者：
deDreuzy, Edouard
Chalishazar, Aditi
Heath, Jack
Margulies, Carrie M.
Labella, John
Viswanathan, Ramya
Loveluck, Katherine
Chang, KaiHsin
Jayaram, Hariharan
Zuris, John A.
Myer, Vic E.
Albright, Charlie
Cotta-Ramusino, Cecilia
Gori, Jennifer L.
机构：
来源：
BLOOD | 2017年 / 130卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
4619
引用
收藏
页数：2
相关论文
共 50 条
  • [41] Nanoparticles targeting hematopoietic stem and progenitor cells: Multimodal carriers for the treatment of hematological diseases
    Cruz, Luis J.
    Rezaei, Somayeh
    Grosveld, Frank
    Philipsen, Sjaak
    Eich, Christina
    FRONTIERS IN GENOME EDITING, 2022, 4
  • [42] Genome accessibility in human hematopoietic stem and progenitor cells (HSPC)
    Gargiulo, Gaetano
    Bucci, Gabriele
    Levy, Sam
    Romanenghi, Mauro
    Urnov, Fyodor
    Fomasari, Lorenzo
    Ballarini, Marco
    Santoro, Fabio
    Pelicci, Pier G.
    Minucci, Saverio
    CELLULAR ONCOLOGY, 2008, 30 (03) : 240 - 241
  • [43] CRISPR-Cas9 Genome Editing of γ-Globin Promoters in Human Hematopoietic Stem Cells to Induce Erythrocyte Fetal Hemoglobin for Treatment of β-Hemoglobinopathies
    Metais, Jean-Yves
    Doerfler, Phillip A.
    Mayuranathan, Thiyagaraj
    Bauer, Daniel E.
    Fowler, Stephanie
    Hsieh, Matthew
    Katta, Varun
    Keriwala, Sagar
    Lazzarotto, Cicera
    Luk, Kevin
    Neel, Michael
    Perry, Scott
    Porter, Shaina
    Ryu, Byoung Y.
    Sharma, Akshay
    Shea, Devlin
    Peters, Samuel
    Tisdale, John F.
    Wolfe, Scot A.
    Woodard, Kaitly Jensen
    Uchida, Naoya
    Wu, Yuxuan
    Yao, Yu
    Zeng, Jing
    Pruett-Miller, Shondra M.
    Tsai, Shengdar Q.
    Weiss, Mitchell J.
    BLOOD, 2019, 134
  • [44] Enhancing prime editing in hematopoietic stem and progenitor cells by modulating nucleotide metabolism
    Levesque, Sebastien
    Cosentino, Andrea
    Verma, Archana
    Genovese, Pietro
    Bauer, Daniel E.
    NATURE BIOTECHNOLOGY, 2024, : 534 - 538
  • [45] Assessing Stealth and Sensed Base Editing in Human Hematopoietic Stem/Progenitor Cells
    Fiumara, Martina
    Ferrari, Samuele
    Javed, Attya Omer
    Beretta, Stefano
    Albano, Luisa
    Merelli, Ivan
    Naldini, Luigi
    MOLECULAR THERAPY, 2022, 30 (04) : 6 - 6
  • [46] Therapeutic Base and Prime Editing in Fanconi Anemia Hematopoietic Stem and Progenitor Cells
    Ugalde, L.
    Karasu, M. E.
    Olalla, B.
    Siegner, S.
    Garcia, L.
    Clemens, A.
    Alvarez, L.
    Pena, I.
    Bueren, J. A.
    Corn, J. E.
    Rio, P.
    HUMAN GENE THERAPY, 2022, 33 (23-24) : A62 - A63
  • [47] Gene Editing of Human Hematopoietic Stem and Progenitor Cells: Promise and Potential Hurdles
    Yu, Kyung-Rok
    Natanson, Hannah
    Dunbar, Cynthia E.
    HUMAN GENE THERAPY, 2016, 27 (10) : 729 - 740
  • [48] Assessing Stealth and Sensed Base Editing in Human Hematopoietic Stem/Progenitor Cells
    Fiumara, Martina
    Ferrari, Samuele
    Omer, Attya
    Beretta, Stefano
    Albano, Luisa
    Merelli, Ivan
    Naldini, Luigi
    BLOOD, 2021, 138
  • [49] Using CRISPR/Cas9 to Edit Hematopoietic Stem and Progenitor Cells
    Seclen, Eduardo
    Chen, Hsu-Yu
    Llewellyn, George N.
    Yang, Su J.
    Chateau, Morgan
    Wang, Cathy X.
    Cannon, Paula M.
    MOLECULAR THERAPY, 2016, 24 : S132 - S132
  • [50] Modulating Nucleotide Metabolism Enhances Prime Editing in Hematopoietic Stem and Progenitor Cells
    Levesque, Sebastien
    Bauer, Daniel E.
    BLOOD, 2023, 142
12345