SUBGROUP ANALYSIS OF PEGVALIASE IN ADULTS WITH PHENYLKETONURIA IN PHASE 3 PRISM STUDIES: EVALUATING EFFICACY AND SAFETY BASED ON PREVIOUS SAPROPTERIN RESPONSE OR DIETARY PHENYLALANINE INTAKE

被引：0

作者：

Vockley, Jerry ^{[1
,2
]}

Zori, Roberto ^{[3
]}

Thomas, Janet A. ^{[4
,5
]}

Stuy, Mary ^{[6
]}

Burton, Barbara K. ^{[7
,8
]}

Longo, Nicola ^{[9
]}

Rosen, Orli ^{[10
]}

Gu, Zhonghu ^{[10
]}

Olbertz, Joy ^{[10
]}

Weng, Haoling H. ^{[10
]}

机构：

[1] Univ Pittsburgh, Pittsburgh, PA USA

[2] Childrens Hosp Pittsburgh, Pittsburgh, PA 15213 USA

[3] Univ Florida Hlth, Gainesville, FL USA

[4] Univ Colorado, Sch Med, Aurora, CO USA

[5] Childrens Hosp Colorado, Aurora, CO USA

[6] Indiana Univ, Indianapolis, IN 46204 USA

[7] Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA

[8] Northwestern Univ, Feinberg Sch Med, Chicago, IL 60611 USA

[9] Univ Utah, Salt Lake City, UT USA

[10] BioMarin Pharmaceut Inc, Novato, CA USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2019年 / 127卷 / 03期

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

139

引用

页码：308 / 308

页数：1

共 42 条

[1] SUBGROUP ANALYSIS OF PEGVALIASE IN ADULTS WITH PHENYLKETONURIA IN PHASE 3 PRISM STUDIES: EVALUATING EFFICACY AND SAFETY BASED ON PREVIOUS SAPROPTERIN RESPONSE OR DIETARY PHENYLALANINE INTAKE
Vockley, Jerry
Zori, Roberto
Thomas, Janet A.
Stuy, Mary
Burton, Barbara K.
Longo, Nicola
Rosen, Orli
Gu, Zhonghu
Olbertz, Joy
Weng, Haoling H.
[J]. MOLECULAR GENETICS AND METABOLISM, 2019, 126 (03) : 332 - 332
[2] PHASE 3 PRISM CLINICAL TRIAL EVALUATING EFFICACY AND SAFETY OF PEGVALIASE FOR TREATMENT OF ADULTS WITH PHENYLKETONURIA
Thomas, J.
Levy, H.
Amato, S.
Vockley, G.
Zori, R.
Dimmock, D.
Harding, C.
Bilder, D.
Weng, H. H.
Olbertz, J.
Merilainen, M.
Jiang, J.
Gupta, S.
Gu, Z.
Larimore, K.
Northrup, H.
[J]. MOLECULAR GENETICS AND METABOLISM, 2018, 123 (03) : 270 - 270
[3] EFFICACY AND SAFETY OF THE RECOMMENDED PEGVALIASE DOSING REGIMEN IN ADULTS WITH PHENYLKETONURIA IN THE PHASE 3 PRISM STUDIES
Sacharow, Stephanie
Northrup, Hope
Whitehall, Kaleigh Bulloch
Rowell, Richard
Lindstrom, Kristin
Burton, Barbara
Thomas, Janet
[J]. MOLECULAR GENETICS AND METABOLISM, 2022, 135 (04) : 296 - 297
[4] Efficacyand safety of the recommended pegvaliase dosing regimen in adults with phenylketonuria in the phase 3 PRISM studies
Lindstrom, K.
Sacharow, S.
Northrup, H.
Whitehall, K. B.
Rowell, R.
Burton, B.
Thomas, J.
[J]. MOLECULAR GENETICS AND METABOLISM, 2022, 136 : S23 - S23
[5] PRISM 301: AN OPEN-LABEL, RANDOMIZED, PHASE 3 CLINICAL TRIAL EVALUATING EFFICACY AND SAFETY OF PEGVALIASE FOR THE TREATMENT OF ADULTS WITH PHENYLKETONURIA
Longo, Nicola
Amato, Stephen
Vocldey, Jerry
Wierenga, Klaas
Li, Hong
Bilder, Deborah
Burton, Barbara
Dimmock, David
Harding, Cary
Posner, John
Thomas, Janet A.
Zori, Roberto
Greblikas, Feriandas
Gu, Zhonghua
Merilainen, Markus
Weng, Haoling H.
Levy, Harvey
[J]. MOLECULAR GENETICS AND METABOLISM, 2016, 117 (03) : 268 - 268
[6] PHASE 3 PRISM CLINICAL TRIALS: EVALUATING CHANGE IN DIET WITH PEGVALIASE TREATMENT IN ADULTS WITH PHENYLKETONURIA
Rohr, Fran
Burton, Barbara K.
Longo, Nicola
Thomas, Janet A.
Harding, Cary O.
Rosen, Orli
Gu, Zhonghu
Olbertz, Joy
Weng, Haoling H.
[J]. MOLECULAR GENETICS AND METABOLISM, 2019, 126 (03) : 323 - 323
[7] PHASE 3 PRISM CLINICAL TRIALS: EVALUATING CHANGE IN DIET WITH PEGVALIASE TREATMENT IN ADULTS WITH PHENYLKETONURIA
Rohr, Fran
Burton, Barbara K.
Longo, Nicola
Thomas, Janet A.
Harding, Cary O.
Rosen, Orli
Gu, Zhonghu
Olbertz, Joy
Weng, Haoling H.
[J]. MOLECULAR GENETICS AND METABOLISM, 2019, 127 (03) : 296 - 297
[8] Association of immune response with efficacy and safety outcomes in adults with phenylketonuria administered pegvaliase in phase 3 clinical trials
Gupta, Soumi
Lau, Kelly
Harding, Cary O.
Shepherd, Gillian
Boyer, Ryan
Atkinson, John P.
Knight, Vijaya
Olbertz, Joy
Larimore, Kevin
Gu, Zhonghu
Li, Mingjin
Rosen, Orli
Zoog, Stephen J.
Weng, Haoling H.
Schweighardt, Becky
[J]. EBIOMEDICINE, 2018, 37 : 366 - 373
[9] Evaluating change in diet with pegvaliase treatment in adults with phenylketonuria: Analysis of phase 3 clinical trial data
Rohr, Fran
Burton, Barbara
Dee, Anne
Harding, Cary O.
Lilienstein, Joshua
Lindstrom, Kristin
Macleod, Erin
Rose, Sarah
Singh, Rani
van Calcar, Sandra
Whitehall, Kaleigh
[J]. MOLECULAR GENETICS AND METABOLISM, 2024, 141 (03)
[10] Efficacy and Safety of Secukinumab in US Patients with Psoriatic Arthritis: A Subgroup Analysis of the Phase 3 FUTURE Studies
Kivitz, Alan J.
Kremer, Joel M.
Legerton III, Clarence W.
Pricop, Luminita
Singhal, Atul
[J]. RHEUMATOLOGY AND THERAPY, 2024, 11 (03) : 675 - 689

← 1 2 3 4 5 →