PHASE 3 PRISM CLINICAL TRIALS: EVALUATING CHANGE IN DIET WITH PEGVALIASE TREATMENT IN ADULTS WITH PHENYLKETONURIA

被引：0
|
作者：
Rohr, Fran [1 ]
Burton, Barbara K. [2 ,3 ]
Longo, Nicola [4 ]
Thomas, Janet A. [5 ,6 ]
Harding, Cary O. [7 ]
Rosen, Orli [8 ]
Gu, Zhonghu [8 ]
Olbertz, Joy [8 ]
Weng, Haoling H. [8 ]
机构：
[1] Boston Childrens Hosp, Boston, MA USA
[2] Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA
[3] Northwestern Univ, Feinberg Sch Med, Chicago, IL 60611 USA
[4] Univ Utah, Salt Lake City, UT USA
[5] Univ Colorado, Sch Med, Aurora, CO USA
[6] Childrens Hosp Colorado, Aurora, CO USA
[7] Oregon Hlth & Sci Univ, Portland, OR 97201 USA
[8] BioMarin Pharmaceut Inc, Novato, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2019年 / 126卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
115
引用
收藏
页码：323 / 323
页数：1
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