PHASE 3 PRISM CLINICAL TRIAL EVALUATING EFFICACY AND SAFETY OF PEGVALIASE FOR TREATMENT OF ADULTS WITH PHENYLKETONURIA

被引：0

作者：

Thomas, J. ^{[1
]}

Levy, H. ^{[2
]}

Amato, S. ^{[3
]}

Vockley, G. ^{[4
]}

Zori, R. ^{[5
]}

Dimmock, D. ^{[6
]}

Harding, C. ^{[7
]}

Bilder, D. ^{[8
]}

Weng, H. H. ^{[9
]}

Olbertz, J. ^{[9
]}

Merilainen, M. ^{[9
]}

Jiang, J. ^{[9
]}

Gupta, S. ^{[9
]}

Gu, Z. ^{[9
]}

Larimore, K. ^{[9
]}

Northrup, H. ^{[10
]}

机构：

[1] Univ Colorado, Sch Med, Aurora, CO USA

[2] Boston Childrens Hosp, Boston, MA USA

[3] Univ Kentucky, Lexington, KY USA

[4] Childrens Hosp Pittsburgh, Pittsburgh, PA 15213 USA

[5] Univ Florida, Gainesville, FL USA

[6] Med Coll Wisconsin, Milwaukee, WI 53226 USA

[7] Oregon Hlth & Sci Univ, Portland, OR 97201 USA

[8] Univ Utah, Salt Lake City, UT USA

[9] BioMarin Pharmaceut Inc, Novato, CA USA

[10] Univ Houston, Sch Med, Houston, TX USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2018年 / 123卷 / 03期

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

115

引用

页码：270 / 270

页数：1

共 50 条

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