Efficacyand safety of the recommended pegvaliase dosing regimen in adults with phenylketonuria in the phase 3 PRISM studies

被引：0
|
作者：
Lindstrom, K. [1 ]
Sacharow, S. [2 ]
Northrup, H. [3 ]
Whitehall, K. B. [1 ]
Rowell, R. [1 ]
Burton, B. [4 ]
Thomas, J. [5 ]
机构：
[1] BioMarin Pharmaceut Inc, Novato, CA USA
[2] Harvard Med Sch, Boston Childrens Hosp, Boston, MA 02115 USA
[3] Univ Texas Hlth Sci Ctr Houston, McGovern Med Sch, Houston, TX 77030 USA
[4] Northwestern Univ, Lurie Childrens Hosp, Feinberg Sch Med, Chicago, IL 60611 USA
[5] Univ Colorado, Sch Med, Aurora, CO USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 136卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
P.34
引用
收藏
页码：S23 / S23
页数：1
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