Natural gene therapy: Somatic reversion in the Wiskott-Aldrich syndrome

被引：0
|
作者：
Davis, Brian R. [1 ,2 ]
DiCola, Michael J. [1 ]
Prokopishyn, Nicole L. [1 ]
Rosenberg, Jonathan B. [1 ]
Moratto, Daniele [3 ]
Muul, Linda M. [3 ]
Candotti, Fabio [3 ]
Blaese, R. Michael [1 ]
机构：
[1] Inst Inherited Dis Res, Newtown, PA USA
[2] Univ Texas Houston, Hlth Sci Ctr, Brown Fdn Inst Mol Med, Ctr Stem Cell Res, Houston, TX USA
[3] NHGRI, NIH, Bethesda, MD 20892 USA
来源：
BLOOD CELLS MOLECULES AND DISEASES | 2008年 / 40卷 / 02期
关键词：
D O I：
10.1016/j.bcmd.2007.10.032
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
22
引用
收藏
页码：261 / 261
页数：1
相关论文
共 50 条
  • [1] Gene Therapy for Wiskott-Aldrich Syndrome
    Bosticardo, Marita
    Ferrua, Francesca
    Cavazzana, Marina
    Aiuti, Alessandro
    CURRENT GENE THERAPY, 2014, 14 (06) : 413 - 421
  • [2] Gene Therapy in Wiskott-Aldrich Syndrome
    Leiner, Peter
    ALLERGO JOURNAL, 2014, 23 (01) : 13 - 13
  • [3] Gene therapy of Wiskott-Aldrich syndrome
    Aiuti, A.
    Marangoni, F.
    Scaramuzza, S.
    Panaroni, C.
    Bosticardo, M.
    Trifari, S.
    Locci, M.
    Draghici, E.
    Galy, A.
    Naldini, L.
    Chiesa, R.
    Dupre, L.
    Villa, A.
    Roncarolo, M. G.
    HAEMATOLOGICA-THE HEMATOLOGY JOURNAL, 2007, 92 (06): : 42 - 42
  • [4] Gene therapy for Wiskott-Aldrich Syndrome
    Aiuti, Alessandro
    HUMAN GENE THERAPY, 2014, 25 (11) : A6 - A7
  • [5] Gene therapy for the Wiskott-Aldrich syndrome
    Galy, Anne
    Thrasher, Adrian J.
    CURRENT OPINION IN ALLERGY AND CLINICAL IMMUNOLOGY, 2011, 11 (06) : 545 - 550
  • [6] Gene therapy for Wiskott-Aldrich syndrome
    Witzel, Maximilian Georg Wolfgang
    Braun, Christian Joerg
    Boztug, Kaan
    Klein, Christoph
    EXPERT OPINION ON ORPHAN DRUGS, 2013, 1 (09): : 705 - 715
  • [7] Somatic reversion in Wiskott-Aldrich syndrome: Case reports and mechanistic insights
    Rikhi, Rashmi
    Basu, Suprit
    Arora, Kanika
    Chan, Koon-Wing
    Jindal, Ankur Kumar
    Rawat, Amit
    Lau, Yu-lung
    Suri, Deepti
    SCANDINAVIAN JOURNAL OF IMMUNOLOGY, 2024, 100 (05)
  • [8] Gene Edition for Wiskott-Aldrich Syndrome Gene Therapy
    Martin, Francisco
    Munoz, Pilar
    Cobo, Marien
    Sanchez-Gilabert, Almudena
    Real, Pedro
    Ramos, Veronica
    Gregory, Philip D.
    Holmes, Michael C.
    Toscano, Miguel G.
    MOLECULAR THERAPY, 2015, 23 : S136 - S136
  • [9] Gene therapy in Wiskott-Aldrich syndrome: The next step?
    Julie Y. Patel
    David P. Huston
    Current Allergy and Asthma Reports, 2005, 5 (5) : 347 - 348
  • [10] Efficacy and safety of gene therapy for Wiskott-Aldrich syndrome
    Galy, Anne
    Corre, Guillaume
    Cavazzana-, Marina
    Hacein-Bey-Abina, Salima
    M S-MEDECINE SCIENCES, 2015, 31 (12): : 1066 - 1069
12345