Natural gene therapy: Somatic reversion in the Wiskott-Aldrich syndrome

被引：0
|
作者：
Davis, Brian R. [1 ,2 ]
DiCola, Michael J. [1 ]
Prokopishyn, Nicole L. [1 ]
Rosenberg, Jonathan B. [1 ]
Moratto, Daniele [3 ]
Muul, Linda M. [3 ]
Candotti, Fabio [3 ]
Blaese, R. Michael [1 ]
机构：
[1] Inst Inherited Dis Res, Newtown, PA USA
[2] Univ Texas Houston, Hlth Sci Ctr, Brown Fdn Inst Mol Med, Ctr Stem Cell Res, Houston, TX USA
[3] NHGRI, NIH, Bethesda, MD 20892 USA
来源：
BLOOD CELLS MOLECULES AND DISEASES | 2008年 / 40卷 / 02期
关键词：
D O I：
10.1016/j.bcmd.2007.10.032
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
22
引用
收藏
页码：261 / 261
页数：1
相关论文
共 50 条
  • [21] Hematopoietic stem cell gene therapy for Wiskott-Aldrich Syndrome
    Boztug, Kaan
    Dewey, Ricardo A.
    Diez, Ines Avedillo
    Manfred, Schmidt
    Kerstin, Schwarzwaelder
    Jana, Diestelhorst
    Sonja, Naundorf
    Klaus, Kuehlke
    Irina, Kondratenko
    Laszlo, Marodi
    von Kalle, Christof
    Welte, Karl
    Klein, Christoph
    BLOOD, 2007, 110 (11) : 155A - 155A
  • [22] Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult
    Morris, Emma C.
    Fox, Thomas
    Chakraverty, Ronjon
    Tendeiro, Rita
    Snell, Katie
    Rivat, Christine
    Grace, Sarah
    Gilmour, Kimberly
    Workman, Sarita
    Buckland, Karen
    Butler, Katie
    Chee, Ronnie
    Salama, Alan D.
    Ibrahim, Hazem
    Hara, Havinder
    Duret, Cecile
    Mavilio, Fulvio
    Male, Frances
    Bushman, Frederick D.
    Galy, Anne
    Burns, Siobhan O.
    Gaspar, H. Bobby
    Thrasher, Adrian J.
    BLOOD, 2017, 130 (11) : 1327 - 1335
  • [23] WISKOTT-ALDRICH SYNDROME
    PRITIKIN, RI
    METABOLIC AND PEDIATRIC OPHTHALMOLOGY, 1980, 4 (02) : 106 - 106
  • [24] The Wiskott-Aldrich syndrome
    Orange, JS
    Stone, KD
    Turvey, SE
    Krzewski, K
    CELLULAR AND MOLECULAR LIFE SCIENCES, 2004, 61 (18) : 2361 - 2385
  • [25] WISKOTT-ALDRICH SYNDROME
    SRIVASTAVA, RN
    ARCHIVES OF DISEASE IN CHILDHOOD, 1967, 42 (226) : 604 - +
  • [26] WISKOTT-ALDRICH SYNDROME
    SHAMY, HK
    HEGGARTY, HJ
    BRITISH JOURNAL OF DERMATOLOGY, 1987, 117 : 52 - 53
  • [27] WISKOTT-ALDRICH SYNDROME
    BARSKY, S
    MOMTAZ, AH
    ARCHIVES OF DERMATOLOGY, 1967, 96 (06) : 730 - &
  • [28] WISKOTT-ALDRICH SYNDROME
    DILERNIA, V
    PATRIZI, A
    RICCI, G
    MASI, M
    PEDIATRIC DERMATOLOGY, 1991, 8 (03) : 251 - 252
  • [29] The Wiskott-Aldrich syndrome
    Hans D. Ochs
    Springer Seminars in Immunopathology, 1998, 19 : 435 - 458
  • [30] Wiskott-Aldrich syndrome
    Pelling, Daniel
    Bain, Barbara J.
    AMERICAN JOURNAL OF HEMATOLOGY, 2024, 99 (05) : 969 - 970
12345