Natural gene therapy: Somatic reversion in the Wiskott-Aldrich syndrome

被引:0
|
作者
Davis, Brian R. [1 ,2 ]
DiCola, Michael J. [1 ]
Prokopishyn, Nicole L. [1 ]
Rosenberg, Jonathan B. [1 ]
Moratto, Daniele [3 ]
Muul, Linda M. [3 ]
Candotti, Fabio [3 ]
Blaese, R. Michael [1 ]
机构
[1] Inst Inherited Dis Res, Newtown, PA USA
[2] Univ Texas Houston, Hlth Sci Ctr, Brown Fdn Inst Mol Med, Ctr Stem Cell Res, Houston, TX USA
[3] NHGRI, NIH, Bethesda, MD 20892 USA
关键词
D O I
10.1016/j.bcmd.2007.10.032
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
22
引用
收藏
页码:261 / 261
页数:1
相关论文
共 50 条
  • [41] Spontaneous in vivo reversion of an inherited mutation in the Wiskott-Aldrich syndrome
    Ariga, T
    Kondoh, T
    Yamaguchi, K
    Yamada, M
    Sasaki, S
    Nelson, DL
    Ikeda, H
    Kobayashi, K
    Moriuchi, H
    Sakiyama, Y
    JOURNAL OF IMMUNOLOGY, 2001, 166 (08): : 5245 - 5249
  • [42] THE WISKOTT-ALDRICH SYNDROME
    PEACOCKE, M
    SIMINOVITCH, KA
    SEMINARS IN DERMATOLOGY, 1993, 12 (03): : 247 - 254
  • [43] THE WISKOTT-ALDRICH SYNDROME
    ORMEROD, AD
    INTERNATIONAL JOURNAL OF DERMATOLOGY, 1985, 24 (02) : 77 - 81
  • [44] WISKOTT-ALDRICH SYNDROME
    WALZER, R
    ARCHIVES OF DERMATOLOGY, 1969, 99 (03) : 372 - +
  • [45] WISKOTT-ALDRICH SYNDROME
    ERTTMANN, R
    THONE, I
    LANDBECK, G
    MONATSSCHRIFT KINDERHEILKUNDE, 1983, 131 (08) : 524 - 527
  • [46] The Wiskott-Aldrich syndrome
    Ochs, HD
    CLINICAL REVIEWS IN ALLERGY & IMMUNOLOGY, 2001, 20 (01) : 61 - 86
  • [47] Wiskott-Aldrich Syndrome
    Kariya, Shin
    Nishizaki, Kazunori
    Paparella, Michael M.
    Cureoglu, Sebahattin
    OTOLOGY & NEUROTOLOGY, 2013, 34 (03) : E16 - E17
  • [48] MUTATIONS WITHIN THE WISKOTT-ALDRICH SYNDROME GENE
    ZHU, QL
    ZHANG, M
    BLAESE, M
    JUNKER, A
    OCHS, HD
    PEDIATRIC RESEARCH, 1995, 37 (04) : A12 - A12
  • [49] Wiskott-Aldrich syndrome
    Notarangelo, Luigi D.
    Miao, Carol H.
    Ochs, Hans D.
    CURRENT OPINION IN HEMATOLOGY, 2008, 15 (01) : 30 - 36
  • [50] The Wiskott-Aldrich syndrome
    Ochs, HD
    Thrasher, AJ
    JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2006, 117 (04) : 725 - 738