共 50 条
- [2] Gene therapy of Wiskott-Aldrich syndrome [J]. HAEMATOLOGICA-THE HEMATOLOGY JOURNAL, 2007, 92 (06): : 42 - 42
- [5] Gene therapy for Wiskott-Aldrich syndrome [J]. EXPERT OPINION ON ORPHAN DRUGS, 2013, 1 (09): : 705 - 715
- [7] Gene Edition for Wiskott-Aldrich Syndrome Gene Therapy [J]. MOLECULAR THERAPY, 2015, 23 : S136 - S136
- [9] Efficacy and safety of gene therapy for Wiskott-Aldrich syndrome [J]. M S-MEDECINE SCIENCES, 2015, 31 (12): : 1066 - 1069
- [10] Gene therapy for Wiskott-Aldrich syndrome: here to stay [J]. LANCET HAEMATOLOGY, 2019, 6 (05): : E230 - E231