AAV9 gene therapy rescues a murine model of Menkes disease

被引:0
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作者
Kaler, Stephen G. [1 ]
Donsante, Anthony [1 ]
Haddad, Marie-Reine [1 ]
机构
[1] NICHD, Program Mol Med, NIH, Bethesda, MD USA
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D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
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页码:A77 / A78
页数:2
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