Gene delivery and biodistribution following intravenous administration of AAV9/rh10 iduronidase in a murine model of MPS type I

被引：0
|
作者：
Belur, Lalitha [1 ]
Thuy An Tran [1 ]
Podetz-Pedersen, Kelly M. [1 ]
Riedl, Maureen [1 ]
Vulchanova, Lucy [1 ]
Kozarsky, Karen [2 ]
Low, Walter C. [1 ]
McIvor, R. Scott [1 ]
机构：
[1] Univ Minnesota, Minneapolis, MN USA
[2] REGENXBIO Inc, Rockville, MD USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2016年 / 117卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2015.12.194
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
36
引用
收藏
页码：S26 / S26
页数：1
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