AAV8 Gene Transfer Rescues a Neonatal Lethal Murine Model of Proprionic Acidemia

被引:0
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作者
Chandler, R. J. [1 ]
Chandrasekaran, S. [1 ]
Venditti, C. P. [1 ]
机构
[1] NHGRI, NIH, Bethesda, MD 20892 USA
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
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页码:1456 / 1456
页数:1
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