Targeted genome editing in human long-term repopulating hematopoietic stem cells for the correction of SCID-X1

被引：0

作者：

Genovese, P. ^{[1
]}

Schiroli, G. ^{[1
,2
]}

Conway, A. ^{[3
]}

Guschin, D. ^{[3
]}

Escobar, G. ^{[1
,2
]}

Di Tomaso, T. ^{[1
]}

Marin, V. ^{[4
]}

Giuliani, E. ^{[4
]}

Firrito, C. ^{[1
]}

Gregory, P. D. ^{[3
]}

Holmes, M. C. ^{[3
]}

Gentner, B. ^{[1
]}

Bovolenta, C. ^{[4
]}

Cost, G. J. ^{[3
]}

Lombardo, A. ^{[1
,2
]}

Naldini, L. ^{[1
,2
]}

机构：

[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

[2] Univ Vita Salute San Raffaele, Milan, Italy

[3] Sangamo BioSci Inc, Richmond, CA USA

[4] MolMed SpA, Milan, Italy

来源：

HUMAN GENE THERAPY | 2015年 / 26卷 / 10期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

OR012

引用

页码：A5 / A6

页数：2

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