Targeted genome editing in human long-term repopulating hematopoietic stem cells for the correction of SCID-X1

被引：0
|
作者：
Genovese, P. [1 ]
Schiroli, G. [1 ,2 ]
Conway, A. [3 ]
Guschin, D. [3 ]
Escobar, G. [1 ,2 ]
Di Tomaso, T. [1 ]
Marin, V. [4 ]
Giuliani, E. [4 ]
Firrito, C. [1 ]
Gregory, P. D. [3 ]
Holmes, M. C. [3 ]
Gentner, B. [1 ]
Bovolenta, C. [4 ]
Cost, G. J. [3 ]
Lombardo, A. [1 ,2 ]
Naldini, L. [1 ,2 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2] Univ Vita Salute San Raffaele, Milan, Italy
[3] Sangamo BioSci Inc, Richmond, CA USA
[4] MolMed SpA, Milan, Italy
来源：
HUMAN GENE THERAPY | 2015年 / 26卷 / 10期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR012
引用
收藏
页码：A5 / A6
页数：2
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