Genome Editing of Long-Term Human Hematopoietic Stem Cells for X-Linked Severe Combined Immunodeficiency

被引：0

作者：

Pavel-Dinu, Mara ^{[1
]}

Wiebking, Volker ^{[1
]}

Dejene, Beruh T. ^{[1
]}

Srifa, Waracharee ^{[1
]}

Mantri, Sruthi ^{[1
]}

Nicolas, Carmencita ^{[1
]}

Lee, Ciaran M. ^{[2
]}

Bao, Gang ^{[3
]}

Kildebeck, Eric ^{[4
]}

Punjya, Niraj Rajiv ^{[5
]}

Sindhu, Camille ^{[1
]}

Inlay, Matthew A. ^{[6
]}

Saxena, Nivedita S. ^{[7
]}

De Ravin, Suk See ^{[8
]}

Malech, Harry L. ^{[8
]}

Roncarolo, Maria Grazia ^{[9
,10
,11
,12
]}

Weinberg, Kenneth ^{[1
]}

Porteus, Matthew ^{[13
]}

机构：

[1] Stanford Univ, Stanford, CA 94305 USA

[2] Rice Univ, Genome Editing Core, Houston, TX 77251 USA

[3] Rice Univ, Houston, TX 77251 USA

[4] Univ Texas Dallas, Richardson, TX 75083 USA

[5] Univ Calif Davis, Davis, CA 95616 USA

[6] Univ Calif Irvine, Irvine, CA 92717 USA

[7] Icahn Sch Med Mt Sinai, New York, NY 10029 USA

[8] NIAID, NIH, 9000 Rockville Pike, Bethesda, MD 20892 USA

[9] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA

[10] Stanford Univ, Sch Med, Med Blood & Marrow Transplantat, Stanford, CA 94305 USA

[11] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA

[12] Stanford Univ, Sch Med, Ctr Definit & Curat Med, Div Stem Cell Transplantat & Regenerat Med,Dept P, Stanford, CA 94305 USA

[13] Stanford Univ, Sch Med, Dept Pediat, Div Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA

来源：

JOURNAL OF CLINICAL IMMUNOLOGY | 2018年 / 38卷 / 03期

关键词：

D O I：

暂无

中图分类号：

R392 [医学免疫学]; Q939.91 [免疫学];

学科分类号：

100102 ;

摘要：

引用

页码：365 / 366

页数：2

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