The burden of Fabry disease in the United States: Results from the Adelphi Fabry Disease Specific Programme

被引：0
|
作者：
Dorling, Patricia [1 ]
Azimpour, Khashayar [2 ]
Mellor, Jennifer [3 ]
Hatchell, Niall [3 ]
Rutherford, Megan [4 ]
Raad, Angie [5 ]
机构：
[1] Chiesi, Boston, MA USA
[2] Chiesi, Woodbridge, ON, Canada
[3] Adelphi Real World, Macclesfield, England
[4] Cytel Inc, London, England
[5] Cytel Inc, Waltham, MA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107809
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
70
引用
收藏
页数：2
相关论文
共 50 条
  • [41] FABRY DISEASE
    BECK, G
    SCHWEIZERISCHE MEDIZINISCHE WOCHENSCHRIFT, 1980, 110 (33) : 1190 - 1201
  • [42] The management and treatment of children with Fabry disease: A United States-based perspective
    Hopkin, Robert J.
    Jefferies, John L.
    Laney, Dawn A.
    Lawson, Victoria H.
    Mauer, Michael
    Taylor, Matthew R.
    Wilcox, William R.
    MOLECULAR GENETICS AND METABOLISM, 2016, 117 (02) : 104 - 113
  • [43] Fabry disease pre-treatment patterns in United States claims data
    Dumitriu, Alexandra
    Miles, Gandarvaka
    Maksimova, Irina
    Crespo, Ana
    Ocampo, Andrea
    Ip, Queeny
    Jordan, Michael
    Petruski-Ivleva, Natalia
    Araujo, Roberto
    MOLECULAR GENETICS AND METABOLISM, 2024, 141 (02)
  • [44] Estimating Fabry disease prevalence and treatment rates in the United States: An epidemiological analysis
    Azimpour, Khashayar
    Dorling, Patricia
    Kunduri, Swati
    Lam, Felix
    De, Atish
    Leinwand, Brian
    MOLECULAR GENETICS AND METABOLISM, 2024, 141 (02)
  • [45] HUMANISTIC BURDEN OF FABRY DISEASE AND ASSOCIATED UTILITY VALUES
    Azimpour, K.
    Dorling, P.
    Igbelina, C. D.
    Kwon, C.
    Rizzo, M.
    VALUE IN HEALTH, 2024, 27 (06) : S320 - S321
  • [46] Red Fabry: First year results of a Spanish pedigree project on Fabry disease
    Barriales-Villa, Roberto
    Aguirre, Javier
    Goicoechea, Marian
    Maria Larranaga-Moreira, Jose
    Perez, Tomas
    Sanchez, Rosario
    MOLECULAR GENETICS AND METABOLISM, 2021, 132 (02) : S19 - S19
  • [47] Fabry disease model: A rational approach to the management of Fabry disease
    Wanner, Christoph
    CLINICAL THERAPEUTICS, 2007, 29 : S2 - S5
  • [48] Fabry disease: experience of screening dialysis patients for Fabry disease
    Eiji Kusano
    Osamu Saito
    Tetsu Akimoto
    Yasushi Asano
    Clinical and Experimental Nephrology, 2014, 18 : 269 - 273
  • [49] Fabry disease: experience of screening dialysis patients for Fabry disease
    Kusano, Eiji
    Saito, Osamu
    Akimoto, Tetsu
    Asano, Yasushi
    CLINICAL AND EXPERIMENTAL NEPHROLOGY, 2014, 18 (02) : 269 - 273
  • [50] Agalsidase alfa: specific treatment for Fabry disease
    Mehta, A
    HOSPITAL MEDICINE, 2002, 63 (06): : 347 - 350
12345