The burden of Fabry disease in the United States: Results from the Adelphi Fabry Disease Specific Programme

被引：0
|
作者：
Dorling, Patricia [1 ]
Azimpour, Khashayar [2 ]
Mellor, Jennifer [3 ]
Hatchell, Niall [3 ]
Rutherford, Megan [4 ]
Raad, Angie [5 ]
机构：
[1] Chiesi, Boston, MA USA
[2] Chiesi, Woodbridge, ON, Canada
[3] Adelphi Real World, Macclesfield, England
[4] Cytel Inc, London, England
[5] Cytel Inc, Waltham, MA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107809
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
70
引用
收藏
页数：2
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