The burden of Fabry disease in the United States: Results from the Adelphi Fabry Disease Specific Programme

被引：0

作者：

Dorling, Patricia ^{[1
]}

Azimpour, Khashayar ^{[2
]}

Mellor, Jennifer ^{[3
]}

Hatchell, Niall ^{[3
]}

Rutherford, Megan ^{[4
]}

Raad, Angie ^{[5
]}

机构：

[1] Chiesi, Boston, MA USA

[2] Chiesi, Woodbridge, ON, Canada

[3] Adelphi Real World, Macclesfield, England

[4] Cytel Inc, London, England

[5] Cytel Inc, Waltham, MA USA

来源：

关键词：

D O I：

10.1016/j.ymgme.2023.107809

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：2

共 50 条

[31] Fabry disease
Schiffmann, Raphael
PHARMACOLOGY & THERAPEUTICS, 2009, 122 (01) : 65 - 77
[32] Fabry disease
Knebel, Fabian
Canaan-Kuehl, Sima
Tillmanns, Christian
Mattig, Isabel
Bekfani, Tarek
Mangner, Norman
Braun-Dullaeus, Ruediger C.
KARDIOLOGE, 2021, 15 (03): : 299 - 314
[33] Fabry disease
Toyooka, Keiko
CURRENT OPINION IN NEUROLOGY, 2011, 24 (05) : 463 - 468
[34] Fabry Disease
Thomas, Alison S.
Hughes, Derralynn A.
PEDIATRIC ENDOCRINOLOGY REVIEWS PER, 2014, 12 : 88 - 101
[35] Fabry disease
Daghfous, A.
Toledano, E.
Kalsoum, E.
Tempremant, F.
Boulanger, T.
Leclerc, X.
Pruvo, J. -P.
DIAGNOSTIC AND INTERVENTIONAL IMAGING, 2015, 96 (03) : 307 - 309
[36] Fabry Disease
Graf, S.
Gatterer, C.
JOURNAL FUR KARDIOLOGIE, 2021, 28 (5-6): : 188 - 189
[37] Fabry disease
Stephan, F.
Haber, R.
ANNALES DE DERMATOLOGIE ET DE VENEREOLOGIE, 2017, 144 (02): : 137 - 146
[38] Fabry disease
Germain, Dominique P.
ORPHANET JOURNAL OF RARE DISEASES, 2010, 5
[39] Fabry disease
Nagueh, SF
HEART, 2003, 89 (08) : 819 - 820
[40] Neuropsychiatric symptoms, disease burden and brain structure in patients with Fabry disease
Schermuly, I.
Mueller, M. J.
Keller, I.
Marin, D.
Albrecht, J.
Beck, M.
Stoeter, P.
Fellgiebel, A.
INTERNATIONAL JOURNAL OF CLINICAL PHARMACOLOGY AND THERAPEUTICS, 2009, 47 : S141 - S141