The burden of Fabry disease in the United States: Results from the Adelphi Fabry Disease Specific Programme

被引：0
|
作者：
Dorling, Patricia [1 ]
Azimpour, Khashayar [2 ]
Mellor, Jennifer [3 ]
Hatchell, Niall [3 ]
Rutherford, Megan [4 ]
Raad, Angie [5 ]
机构：
[1] Chiesi, Boston, MA USA
[2] Chiesi, Woodbridge, ON, Canada
[3] Adelphi Real World, Macclesfield, England
[4] Cytel Inc, London, England
[5] Cytel Inc, Waltham, MA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2023.107809
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
70
引用
收藏
页数：2
相关论文
共 50 条
  • [1] Burden of flares on patients with moderate to severe psoriasis: results of the Adelphi Real World Psoriasis Disease Specific Programme in the United States
    Hsu, Ming-Ann
    Lucas, James
    Wood, Robert
    Cappelleri, Joseph C.
    Piercy, James
    Mallbris, Lotus
    Mamolo, Carla
    JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2015, 135 : S34 - S34
  • [2] DISEASE BURDEN, TREATMENT LANDSCAPE, AND HEALTH RELATED QUALITY OF LIFE OUTCOMES IN MYASTHENIA GRAVIS: RESULTS FROM THE ADELPHI REAL WORLD DISEASE SPECIFIC PROGRAMME IN THE UNITED STATES AND EUROPE
    Gray, C.
    Greene, N.
    De Courcy, J.
    Shor, S.
    Anson, L.
    Gibson, G.
    VALUE IN HEALTH, 2023, 26 (06) : S196 - S196
  • [3] Frequency and prevalence of flares in psoriasis: results of the Adelphi Real World Psoriasis Disease Specific Programme in the United States
    Mamolo, Carla
    Lucas, James
    Wood, Robert
    Cappelleri, Joseph C.
    Piercy, James
    Mallbris, Lotus
    Hsu, Ming-Ann
    JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2015, 135 : S2 - S2
  • [4] Patients with Fabry disease on dialysis in the United States
    Thadhani, R
    Wolf, M
    West, ML
    Tonelli, M
    Ruthazer, R
    Pastores, GM
    Obrador, GT
    KIDNEY INTERNATIONAL, 2002, 61 (01) : 249 - 255
  • [5] ECONOMIC BURDEN OF FABRY DISEASE IN COLOMBIA
    Upegui Pachon, A.
    Becerra, J.
    Salgado, S.
    Romero, M.
    Diaz, A.
    Sanchez, V
    Londono, S.
    VALUE IN HEALTH, 2024, 27 (06) : S115 - S115
  • [6] Burden of Valvular Heart Disease in Patients with Fabry Disease
    Yogasundaram, Haran
    Nikhanj, Anish
    Chatur, Safia
    Qi, Arthur
    Hagen, Leanne
    Bailey, Laurie
    Khan, Aneal
    Hopkin, Robert J.
    Khan, Aneal
    Fine, Nowell M.
    Jefferies, John L.
    Oudit, Gavin Y.
    JOURNAL OF THE AMERICAN SOCIETY OF ECHOCARDIOGRAPHY, 2022, 35 (02) : 236 - 238
  • [7] Biologic and Targeted Synthetic DMARD Utilization in the United States: Adelphi Real World Disease Specific Programme for Rheumatoid Arthritis
    Holdsworth, Elizabeth A.
    Donaghy, Bethany
    Fox, Kathleen M.
    Desai, Pooja
    Collier, David H.
    Furst, Daniel E.
    RHEUMATOLOGY AND THERAPY, 2021, 8 (04) : 1637 - 1649
  • [8] Fabry or Anderson Fabry disease
    June, Diana
    EUROPEAN HEART JOURNAL, 2013, 34 (19) : 1387 - 1388
  • [9] The underdiagnosed kidney burden of Fabry disease in females
    Chandramohan, Deepak
    Moreman, Marcus
    Madi, Salam
    Huma, Fatima
    Ahmad, Massoud
    Singleton, Christina
    Warnock, David G.
    Wallace, Eric
    JOURNAL OF TRANSLATIONAL GENETICS AND GENOMICS, 2024, 8 (04) : 394 - 404
  • [10] Lymphedema and Fabry disease: A report from the Fabry registry
    Long, Katie
    Finegold, David
    Graham, Michele
    MOLECULAR GENETICS AND METABOLISM, 2011, 102 (02) : S26 - S26
12345