共 50 条
- [21] NEUROPATHY IMPAIRMENT AND NUTRITIONAL STATUS WITH EPLONTERSEN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSISJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2024, 29 : S138 - S138Conceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalWixner, Jonas论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Umea, Sweden Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal论文数: 引用数: h-index:机构:Adams, David论文数: 0 引用数: 0 h-index: 0机构: Hop Bicetre, Le Kremlin Bicetre, France Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalAttarian, Shahram论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalGillmore, Julian论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, London, England Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalDyck, P. James论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Neurol, Rochester, MN USA Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Santo Antonio, Porto, Portugal ERN NMD, Paris, France Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalChen, Jersey论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalHardy, Elise论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MD USA Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalKwoh, Jesse论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Carlsbad, CA USA Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalNatman, Jonatan论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Global Evidence, BioPharmaceut Med, Gothenburg, Sweden Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, PortugalCruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Amyloidosis Ctr, CEPARM, Univ Hosp, Rio De Janeiro, Brazil Hosp Santa Maria, Ctr Hosp Univ Lisboa Norte, Lisbon, Portugal
- [22] Patisiran treatment in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy after liver transplantationAMERICAN JOURNAL OF TRANSPLANTATION, 2022, 22 (06) : 1646 - 1657论文数: 引用数: h-index:机构:Wixner, Jonas论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyPlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: East Paris Univ, Hosp Henri Mondor, Publ Assistance Hosp Paris, Dept Neurol, Creteil, France INSERM, U955 Team Biol Neuromuscular Syst 10, Mondor Biomed Res Inst IMRB, Creteil, France Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyMunoz-Beamud, Francisco论文数: 0 引用数: 0 h-index: 0机构: Juan Ramon Jimenez Hosp, Dept Internal Med, Hereditary Amyloidosis Unit, Huelva, Spain Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, Germany论文数: 引用数: h-index:机构:Gillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, Div Med, Med Sch, London, England Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyMazzeo, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, Dept Clin & Expt Med, Unit Neurol & Neuromuscular Dis, Messina, Italy Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyLi, Xingyu论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyJay, Patrick Y.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut Inc, Cambridge, MA USA Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, GermanyAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Neurol Dept, INSERM, U1195, Le Kremlin Bicetre, France CHU Bicetre, AP HP, Neurol Dept, Le Kremlin Bicetre, France Univ Duisburg Essen, Univ Hosp Essen, Dept Gastroenterol Hepatol & Transplant Med, Essen, Germany
- [23] Neuropathy impairment and nutritional status with eplontersen in patients with hereditary transthyretin-mediated amyloidosisAMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2024, 31 : S68 - S68Wixner, Jonas论文数: 0 引用数: 0 h-index: 0机构: Umea Univ, Umea, Sweden Umea Univ, Dept Publ Hlth & Clin Med, Umea, Sweden Umea Univ, Umea, SwedenConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Governo Republ Portuguesa, Lisbon, Portugal Umea Univ, Umea, Sweden论文数: 引用数: h-index:机构:Adams, David论文数: 0 引用数: 0 h-index: 0机构: Republ Francaise, Paris, France Umea Univ, Umea, SwedenPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Umea Univ, Umea, SwedenShahram, Attarian论文数: 0 引用数: 0 h-index: 0机构: Timone Univ Hosp, Referral Ctr Neuromuscular Dis & ALS, APHM, Marseille, France Umea Univ, Umea, SwedenGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: Euro NMD, Filnemus, Marseille, France Univ London, London, England Umea Univ, Umea, SwedenDyck, P. James B.论文数: 0 引用数: 0 h-index: 0机构: Mayo Fdn Med Educ & Res, Rochester, MN USA Umea Univ, Umea, SwedenCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Santo Antonio, Unidade Corino Andrade, Porto, Portugal Umea Univ, Umea, SwedenChen, Jersey论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA Umea Univ, Umea, SwedenHardy, Elise论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA Umea Univ, Umea, SwedenKwoh, Jesse论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA Umea Univ, Umea, SwedenNatman, Jonatan论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, BioPharmaceut R, Gaithersburg, MD USA Umea Univ, Umea, SwedenCruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA Umea Univ, Umea, Sweden
- [24] HELIOS-A: RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHYJOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, 2022, 79 (09) : 302 - 302Gonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoAdams, David论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoTournev, Ivailo论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoTaylor, Mark论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoPlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoBerk, John论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoGillmore, Julian David论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoLow, Soon-Chai论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoSekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoChen, Chongshu论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoBadri, Prajakta论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoArum, Seth论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoVest, John论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, MexicoPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico
- [25] HELIOS-A: 9-MONTH RESULTS FROM THE RANDOMIZED TREATMENT EXTENSION PERIOD OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHYJOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2023, 28 : S40 - S40Obici, Laura论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, Italy IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyPolydefkis, Michael论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyGonzalez-Duarte, Alejandra论文数: 0 引用数: 0 h-index: 0机构: Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Neurol, Mexico City, DF, Mexico IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyWaddington-Cruz, Marcia论文数: 0 引用数: 0 h-index: 0机构: Fed Univ Rio De Janeiro UFRJ, Clementino Fraga Filho Univ Hosp, Rio De Janeiro, Brazil IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalySekijima, Yoshiki论文数: 0 引用数: 0 h-index: 0机构: Shinshu Univ, Dept Med, Neurol Rheumatol, Sch Med, Matsumoto, Nagano, Japan IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyGillmore, Julian D.论文数: 0 引用数: 0 h-index: 0机构: UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyYureneva, Elena论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyBadri, Prajakta论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyChen, Chongshu论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalySweetser, Marianne论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyVest, John论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, ItalyAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Neurol Dept, APHP, CHU Bicetre, Paris, France IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, Italy
- [26] Effectiveness of patisiran after switching from tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathyEUROPEAN JOURNAL OF NEUROLOGY, 2024, 31 (09)Labeyrie, Celine论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceMerkel, Madeline论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSethi, Sakshi论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FrancePopadic, Lyuba论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceYang, Hongbo论文数: 0 引用数: 0 h-index: 0机构: Anal Grp, Boston, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceSweetser, Marianne T.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceLin, Hollis论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, FranceAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France Univ Paris Saclay, Assistance Publ Hop Paris AP HP, Ctr Hosp Univ CHU Bicetre, Neurol Dept,CERAMIC,INSERM U1195, 78,Ave Gen Leclerc, F-94270 Le Kremlin Bicetre, France
- [27] LONGTERM TREATMENT EFFECTS OF INOTERSEN ON QUALITY OF LIFE IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHYMUSCLE & NERVE, 2021, 64 : S57 - S57Brown, Duncan论文数: 0 引用数: 0 h-index: 0Karam, Chafic论文数: 0 引用数: 0 h-index: 0Yang, Min论文数: 0 引用数: 0 h-index: 0Done, Nicolae论文数: 0 引用数: 0 h-index: 0Zhu, JingJing论文数: 0 引用数: 0 h-index: 0Greatsinger, Ali论文数: 0 引用数: 0 h-index: 0Bozas, Ana论文数: 0 引用数: 0 h-index: 0Llonch, Montserrat Vera论文数: 0 引用数: 0 h-index: 0Signorovitch, James论文数: 0 引用数: 0 h-index: 0
- [28] Effect of RNAi therapeutics patisiran and vutrisiran on orthostatic hypotension due to dysautonomia in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathyEUROPEAN HEART JOURNAL, 2022, 43 : 2625 - 2625Slama, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, France Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceObici, L.论文数: 0 引用数: 0 h-index: 0机构: IRCCS Fdn Policlin San Matteo, Amyloidosis Res & Treatment Ctr, Pavia, Italy Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceOkumura, T.论文数: 0 引用数: 0 h-index: 0机构: Nagoya Univ, Grad Sch Med, Dept Cardiol, Nagoya, Aichi, Japan Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceArum, S.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceHale, C.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceJay, P. Y.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceCapocelli, K.论文数: 0 引用数: 0 h-index: 0机构: Alnylam Pharmaceut, Cambridge, MA USA Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, FranceGonzalez-Duarte, A.论文数: 0 引用数: 0 h-index: 0机构: Inst Nacl Ciencias Med & Nutr Salvador Zubiran, Mexico City, DF, Mexico Univ Paris Saclay, Cardiol Dept, Hop Bichat, Paris, France
- [29] Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansformJOURNAL OF NEUROLOGY, 2024, 271 (10) : 6655 - 6666Conceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, Portugal Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalBerk, John L.论文数: 0 引用数: 0 h-index: 0机构: Boston Univ, Sch Med, Boston, MA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalWeiler, Markus论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ Hosp, Amyloidosis Ctr, Heidelberg, Germany Heidelberg Univ Hosp, Dept Neurol, Heidelberg, Germany Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalKowacs, Pedro A.论文数: 0 引用数: 0 h-index: 0机构: Inst Neurol Curitiba, Curitiba, PR, Brazil Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalDasgupta, Noel R.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalKhella, Sami论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Sch Med, Philadelphia, PA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalChao, Chi-Chao论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Taipei, Taiwan Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalAttarian, Shahram论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ La Timone, Neuromuscular Disorders & ALS Dept, Marseille, France Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalKwoh, T. Jesse论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalJung, Shiangtung W.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalChen, Jersey论文数: 0 引用数: 0 h-index: 0机构: AstraZeneca, Late Stage Dev Cardiovasc Renal & Metab, BioPharmaceut R&D, Gaithersburg, MA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalViney, Nicholas J.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Clin Dev, Carlsbad, CA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalYu, Rosie Z.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut Inc, Preclin Dev, Carlsbad, CA USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalGertz, Morie论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalMasri, Ahmad论文数: 0 引用数: 0 h-index: 0机构: OHSU Ctr Hypertroph Cardiomyopathy & Amyloidosis, Portland, OR USA Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalCruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Rio de Janeiro, Univ Hosp, Amyloidosis Ctr, CEPARM, Rio De Janeiro, Brazil Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, PortugalCoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Univ Santo Antonio, Porto, Portugal Univ Lisbon, ULS Santa Maria, CAML, Inst Med Mol,Fac Med, Lisbon, Portugal
- [30] Patisiran, an RNAi therapeutic for the treatment of hereditary transthyretin-mediated amyloidosisNEURODEGENERATIVE DISEASE MANAGEMENT, 2019, 9 (01) : 5 - 24Kristen, Arnt, V论文数: 0 引用数: 0 h-index: 0机构: Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, Germany Cardiovasc Ctr Darmstadt, D-64287 Darmstadt, Germany Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, GermanyAjroud-Driss, Senda论文数: 0 引用数: 0 h-index: 0机构: Northwestern Univ, Dept Neurol, Feinberg Sch Med, Chicago, IL 60611 USA Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, GermanyConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Univ Lisbon, Ctr Hosp Lisboa Norte, Hosp Santa Maria, Fac Med, P-1649028 Lisbon, Portugal Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, GermanyGorevic, Peter论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, Dept Med, New York, NY 10029 USA Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, GermanyKyriakides, Theodoros论文数: 0 引用数: 0 h-index: 0机构: Cyprus Inst Neurol & Genet, CY-1683 Nicosia, Cyprus Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, GermanyObici, Laura论文数: 0 引用数: 0 h-index: 0机构: Fdn IRCCS Policlin San Matteo, Amyloidosis Res & Treatment Ctr, I-27100 Pavia, Italy Heidelberg Univ, Dept Cardiol, D-69120 Heidelberg, Germany