HELIOS-A: 9-MONTH RESULTS FROM THE RANDOMIZED TREATMENT EXTENSION PERIOD OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY

被引:0
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作者
Obici, Laura [1 ]
Polydefkis, Michael [2 ]
Gonzalez-Duarte, Alejandra [3 ]
Waddington-Cruz, Marcia [4 ]
Sekijima, Yoshiki [5 ]
Gillmore, Julian D. [6 ]
Yureneva, Elena [7 ]
Badri, Prajakta [7 ]
Chen, Chongshu [7 ]
Sweetser, Marianne [7 ]
Vest, John [7 ]
Adams, David [8 ]
机构
[1] IRCCS Fondat, Amyloidosis Res & Treatment Ctr, Policlin San Matteo, Pavia, Italy
[2] Johns Hopkins Univ, Sch Med, Dept Neurol, Baltimore, MD 21205 USA
[3] Natl Inst Med Sci & Nutr Salvador Zubiran INCMNSZ, Neurol, Mexico City, DF, Mexico
[4] Fed Univ Rio De Janeiro UFRJ, Clementino Fraga Filho Univ Hosp, Rio De Janeiro, Brazil
[5] Shinshu Univ, Dept Med, Neurol Rheumatol, Sch Med, Matsumoto, Nagano, Japan
[6] UCL, Royal Free Hosp, Natl Amyloidosis Ctr, London, England
[7] Alnylam Pharmaceut, Cambridge, MA USA
[8] Univ Paris Saclay, Neurol Dept, APHP, CHU Bicetre, Paris, France
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R74 [神经病学与精神病学];
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页码:S40 / S40
页数:1
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