SIMULATED TREATMENT COMPARISON AND MATCHINGADJUSTED INDIRECT COMPARISON OF THE EFFICACY OF EPLONTERSEN AND VUTRISIRAN FOR THE TREATMENT OF HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY

被引:0
|
作者
Karam, C. [1 ]
Gillmore, J. D. [2 ]
Chen, G. [3 ]
Jenkins, N. C. [4 ]
Hale, M. J. [4 ]
Chen, J. [5 ]
Viney, N. J. [6 ]
Schneider, E. [6 ]
机构
[1] Univ Penn, Dept Neurol, Philadelphia, PA USA
[2] UCL, Royal Free Hosp, Div Med, Natl Amyloidosis Ctr, London, England
[3] AstraZeneca, Cambridge, England
[4] Hlth Econ & Outcomes Res Ltd, Cardiff, Wales
[5] AstraZeneca, Gaithersburg, MD USA
[6] Ionis Pharmaceut Inc, Carlsbad, CA USA
关键词
D O I
暂无
中图分类号
F [经济];
学科分类号
02 ;
摘要
CO183
引用
收藏
页码:S46 / S47
页数:2
相关论文
共 50 条
  • [31] COST OF INOTERSEN AND PATISIRAN FOR THE TREATMENT OF ADULTS WITH POLYNEUROPATHY OF HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS IN CANADA, GERMANY, AND ITALY
    Brown, D.
    Vera-Llonch, M.
    Shaff, M.
    Rolli, A.
    Vega, M.
    Blum, M.
    Nestler-Parr, S.
    Jiresch, M.
    Weycker, D.
    VALUE IN HEALTH, 2020, 23 : S606 - S607
  • [32] Eplontersen for hereditary transthyretin amyloidosis with polyneuropathy: an exploratory analysis of treatment effect in male and female patients
    Cruz, Marcia Waddington
    Berk, John
    Parman, Yesim
    Gertz, Morie
    Khella, Sami
    Weiler, Markus
    Kwoh, Jesse
    Chen, Jersey
    Reicher, Barry
    Natmani, Jonatan
    Dasgupta, Noel R.
    AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, 2024, 31 : S81 - S81
  • [33] Kidney Function And Proteinuria With Eplontersen Treatment For Hereditary Transthyretin Amyloidosis
    Maurer, Mathew s
    Gillmore, Julian D.
    Berk, John l
    Masri, Ahmad
    DA Silva, Moises dias
    Kwoh, Jesse
    Littl, Dustin j
    Natman, Jonatan
    Zhou, Wunan
    Waddington-cruz, Marcia
    JOURNAL OF CARDIAC FAILURE, 2025, 31 (01) : 346 - 347
  • [34] HELIOS-A: IMPACT OF VUTRISIRAN ON QUALITY OF LIFE AND FUNCTIONAL STATUS IN HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS
    Ajroud-Driss, Senda
    Berk, John L.
    Adams, David
    Gillmore, Julian
    Lin, Kon-Ping
    Kale, Parag
    Koike, Haruki
    Aldinc, Emre
    Chen, Chongshu
    Vest, John
    Obici, Laura
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2023, 28 : S40 - S41
  • [35] Familial amyloidotic polyneuropathy: current and emerging treatment options for transthyretin-mediated amyloidosis
    Hund, Ernst
    APPLICATION OF CLINICAL GENETICS, 2012, 5 : 37 - 41
  • [36] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
    Adams, Davide
    Tournev, Ivailo
    Taylor, Mark
    Coelho, Teresa
    Plante-Bordeneuve, Violaine
    Berk, John
    Gonzalez-Duarte, Alejandra
    Gillmore, Julian
    Low, Soon-Chai
    Sekijima, Yoshiki
    Obici, Laura
    Blakesley, Rick
    Arum, Seth
    Shilling, Rebecca
    Vest, John
    Polydefkis, Michael
    JOURNAL OF THE NEUROLOGICAL SCIENCES, 2021, 429
  • [37] HELIOS-A: NINE-MONTH RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
    Adams, David
    Tournev, Ivailo
    Taylor, Mark
    Coelho, Teresa
    Plante-Bordeneuve, Violaine
    Berk, John
    Gonzalez-Duarte, Alejandra
    Gillmore, Julian
    Low, Soon-Chai
    Sekijima, Yoshiki
    Obici, Laura
    Blakesley, Rick
    Arum, Seth
    Shilling, Rebecca
    Vest, John
    Polydefkis, Michael
    MUSCLE & NERVE, 2021, 64 : S54 - S55
  • [38] HELIOS-A: 9-month Results from the Phase 3 Study of Vutrisiran in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
    Adams, David
    Tournev, Ivailo L.
    Taylor, Mark S.
    Coelho, Teresa
    Plante-Bordeneuve, Violaine
    Berk, John L.
    Gonzalez-Duarte, Alejandra
    Gillmore, Julian D.
    Low, Soon-Chai
    Sekijima, Yoshiki
    Obici, Laura
    Blakesley, Rick
    Arum, Seth
    Shilling, Rebecca
    Vest, John
    Polydefkis, Michael
    NEUROLOGY, 2021, 96 (15)
  • [39] Practical Guidance for the Use of Patisiran in the Management of Polyneuropathy in Hereditary Transthyretin-Mediated Amyloidosis
    Dixon, Stacy
    Kang, Xuan
    Quan, Dianna
    THERAPEUTICS AND CLINICAL RISK MANAGEMENT, 2023, 19 : 973 - 981
  • [40] HELIOS-A: 9-month results from the phase 3 study of vutrisiran in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy
    Adams, David
    Tournev, Ivailo
    Taylor, Mark
    Coelho, Teresa
    Plante-Bordeneuve, Violaine
    Berk, John
    Gonzalez-Duarte, Alejandra
    Gillmore, Julian
    Low, Soon-Chai
    Sekijima, Yoshiki
    Obici, Laura
    Blakesley, Rick
    Arum, Seth
    Shilling, Rebecca
    Vest, John
    Polydefkis, Michael
    JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, 2021, 26 (03) : 309 - 309