Developing an AAV-Based Gene Replacement Therapy for Mitochondrial Alanyl-tRNA Synthetase 2 (AARS2) Leukodystrophy

被引：0
|
作者：
Xing, Ruxiao [1 ]
Ren, Lingzhi [1 ]
Liu, Nan [1 ]
Zhou, Chen [1 ]
Liang, Jialing [1 ]
Wang, Jiaming [1 ,2 ]
Gao, Guangping [1 ,2 ]
Wang, Dan [1 ,3 ]
机构：
[1] Univ Massachusetts, Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA
[2] Univ Massachusetts, Dept Microbiol & Physiol Syst, Chan Med Sch, Worcester, MA 01605 USA
[3] Univ Massachusetts, RNA Therapeut Inst, Chan Med Sch, Worcester, MA 01605 USA
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
36
引用
收藏
页码：20 / 20
页数：1
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