Mitochondrial gene therapy: AAV2-mediated direct delivery of nucleic acids to the mitochondrial matrix as a treatment for Lebers Hereditary Optic Neuropathy

被引：0
|
作者：
Huston, M. W. [1 ]
Mastroberardino, P. G. [2 ]
Wagemaker, G. [3 ]
de Coo, I. F. M. [1 ]
机构：
[1] Erasmus Univ, Med Ctr, Dept Neurol, Rotterdam, Netherlands
[2] Erasmus Univ, Med Ctr, Dept Genet, Rotterdam, Netherlands
[3] Hacettepe Univ, Stem Cell Res Ctr, Ankara, Turkey
来源：
HUMAN GENE THERAPY | 2014年 / 25卷 / 11期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P153
引用
收藏
页码：A105 / A105
页数：1
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