Preclinical Development of an AAV-Based Gene Therapy (OTO-825) for Congenital Hearing Loss Due to GJB2 Deficiency

被引：0
|
作者：
Uribe, Phillip [1 ]
Mathur, Pranav D. [1 ]
Wang, Xiaobo [1 ]
Rosenberg, David [1 ]
Siegel, Sairey [1 ]
Barden, Jeremy [1 ]
Bartolome, Christopher [2 ]
Jaramillo, David [2 ]
Harrop-Jones, Anne [1 ]
Fernandez, Rayne [1 ]
Vestal, James [1 ]
Pastenes, Rodrigo [1 ]
Szobota, Stephanie [1 ]
Piu, Fabrice [1 ]
Simic, Damir [2 ]
Pennock, Steven [2 ]
Shearman, Mark [2 ]
Scaria, Abraham [2 ]
Jacques, Bonnie [1 ]
Foster, Alan C. [1 ]
机构：
[1] Otonomy, San Diego, CA USA
[2] Appl Genet Technol Corp, Alachua, FL USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1226
引用
收藏
页码：571 / 571
页数：1
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