A comparison of immediate release and delayed release cysteamine in 17 patients with nephropathic cystinosis

被引：0
|
作者：
Christina van Stein
Sabrina Klank
Marianne Grüneberg
Chris Ottolenghi
Jürgen Grebe
Janine Reunert
Erik Harms
Thorsten Marquardt
机构：
[1] University of Muenster,Department of General Pediatrics, Metabolic Diseases
[2] Université Paris Descartes,UMR 1163
[3] Sorbonne Paris Cité,Biochimie Métabolique et Protéomique
[4] Institut IMAGINE,undefined
[5] Hôpital Necker – Enfants Malades,undefined
来源：
Orphanet Journal of Rare Diseases | / 16卷
关键词：
Nephropathic cystinosis; Immediate-release cysteamine; Delayed-release cysteamine;
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