A comparison of immediate release and delayed release cysteamine in 17 patients with nephropathic cystinosis

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作者
Christina van Stein
Sabrina Klank
Marianne Grüneberg
Chris Ottolenghi
Jürgen Grebe
Janine Reunert
Erik Harms
Thorsten Marquardt
机构
[1] University of Muenster,Department of General Pediatrics, Metabolic Diseases
[2] Université Paris Descartes,UMR 1163
[3] Sorbonne Paris Cité,Biochimie Métabolique et Protéomique
[4] Institut IMAGINE,undefined
[5] Hôpital Necker – Enfants Malades,undefined
关键词
Nephropathic cystinosis; Immediate-release cysteamine; Delayed-release cysteamine;
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