Long-Term Rescue of a Hypomorphic Lethal Murine Model of Citrullinemia Type I by Liver-Directed, AAV8-Mediated Gene Therapy

被引：0
|
作者：
Wang, Lili [1 ,2 ]
White, John [3 ]
He, Zhenning [3 ]
McMenamin, Deirdre [3 ]
Wilson, James M. [3 ]
机构：
[1] Univ Penn, Dept Pathol, Gene Therapy Program, Philadelphia, PA 19104 USA
[2] Univ Penn, Lab Med, Philadelphia, PA 19104 USA
[3] Univ Penn, Dept Med, Gene Therapy Program, Philadelphia, PA 19104 USA
来源：
MOLECULAR THERAPY | 2017年 / 25卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
242
引用
收藏
页码：114 / 114
页数：1
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