Long-term correction of hyperphenylalaninemia following liver-directed, AAV2/8-mediated gene therapy in murine phenylketonuria

被引：0
|
作者：
Harding, C. O.
Gillingham, M. B.
Bird, A.
Koeberl, D. D.
机构：
[1] Oregon Hlth & Sci Univ, Dept Mol & Med Genet, Portland, OR USA
[2] Duke Univ, Dept Pediat, Durham, NC 27706 USA
来源：
JOURNAL OF INHERITED METABOLIC DISEASE | 2006年 / 29卷
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D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
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页码：30 / 30
页数：1
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