Persistent Correction of Hyperphenylalaninemia Following Liver-Directed, rAAV2/8-Mediated Gene Therapy for Murine Phenylketonuria (PKU)

被引：0
|
作者：
Harding, Cary O. [1 ]
Gillingham, Melanie B. [1 ]
Daghighi, Elizabeth [1 ]
Bird, Andrew [2 ]
Koeberl, Dwight D. [2 ]
机构：
[1] Oregon Hlth & Sci Univ, Portland, OR 97201 USA
[2] Duke Univ, Sch Med, Durham, NC USA
来源：
MOLECULAR THERAPY | 2006年 / 13卷
关键词：
D O I：
10.1016/j.ymthe.2006.08.244
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
219
引用
收藏
页码：S84 / S84
页数：1
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    Harding, C. O.
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  • [7] CORRECTION OF MURINE PHENYLKETONURIA FOLLOWING LIVER-DIRECTED ADMINISTRATION OF A NOVEL RECOMBINANT ADENO-ASSOCIATED VIRUS SEROTYPE 8 (RAAV2/8) VECTOR THAT DIRECTS SITE-SPECIFIC INTEGRATION INTO RIBOSOMAL DNA
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    [J]. Gene Therapy, 2009, 16 : 820 - 823
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