AN OPEN LABEL PHASE 1/2 CLINICAL TRIAL FOR AAV8-MEDIATED LIVER-DIRECTED GENE THERAPY IN ADULTS WITH GLYCOGEN STORAGE DISEASE TYPE IA

被引：0
|
作者：
Weinstein, David A. [1 ,2 ]
Ahmad, Ayesha [3 ]
Poma, Allen [4 ]
Crombez, Eric [4 ]
机构：
[1] Univ Connecticut, Hartford, CT 06112 USA
[2] Connecticut Childrens Med Ctr, Hartford, CT USA
[3] Univ Michigan, Ann Arbor, MI 48109 USA
[4] Ultragenyx Gene Therapy, Cambridge, MA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2019年 / 127卷 / 03期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
141
引用
收藏
页码：309 / 309
页数：1
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