A Novel AAV-Based Gene Therapy for Spinal Muscular Atrophy

被引：0

作者：

Wu, Zhenhua ^{[1
]}

Zhu, Peixin ^{[1
]}

Wang, Qingzeng ^{[1
]}

Li, Zhongwan ^{[1
]}

Chen, Shuyuan ^{[1
]}

Dai, Li ^{[1
]}

Li, Junhui ^{[1
]}

Wang, Lijun ^{[1
]}

Ye, Guojie ^{[1
]}

机构：

[1] Exegenesis Bio Inc, Spring House, PA USA

来源：

MOLECULAR THERAPY | 2022年 / 30卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

541

引用

页码：257 / 257

页数：1

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