Gene therapy rescues newborns with spinal muscular atrophy

被引:7
|
作者
Sheridan, Cormac
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D O I
10.1038/nbt0818-669
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
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页码:669 / 670
页数:2
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