rAAV2/2-ND4 for the Treatment of Leber Hereditary Optic Neuropathy (LHON): 72-Week Data from the REVERSE Phase III Clinical Trial

被引：0

作者：

Yu-Wai-Man, Patrick ^{[1
,2
]}

Moster, Mark ^{[3
,4
,5
]}

Sadun, Alfredo A. ^{[6
,7
]}

Klopstock, Thomas ^{[8
]}

Vignal-Clermont, Catherine ^{[9
,10
]}

Newman, Nancy J. ^{[11
,12
,13
]}

Sergott, Robert C. ^{[14
]}

Carelli, Valerio ^{[15
,16
]}

Chevalier, Caroline ^{[17
]}

Blouin, Laure ^{[17
]}

Taiel, Magali ^{[17
]}

Katz, Barrett ^{[17
]}

Sahel, Jose Alain ^{[18
,19
]}

机构：

[1] Univ Cambridge, Dept Clin Neurosci, Cambridge, England

[2] Moorfields Eye Hosp, London, England

[3] Wills Eye Hosp & Res Inst, Dept Neuroophthalmol, Philadelphia, PA USA

[4] Thomas Jefferson Univ, Dept Neurol, Sidney Kimmel Med Coll, Philadelphia, PA 19107 USA

[5] Thomas Jefferson Univ, Dept Ophthalmol, Sidney Kimmel Med Coll, Philadelphia, PA 19107 USA

[6] Doheny Eye Inst, 1355 San Pablo St, Los Angeles, CA 90033 USA

[7] Univ Calif Los Angeles, Dept Ophthalmol, Los Angeles, CA USA

[8] Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany

[9] Ctr Hosp Natl Ophtalmol Quinze Vingts, Paris, France

[10] Fdn Ophtalmol Rothschild, Paris, France

[11] Emory Univ, Sch Med, Dept Ophthalmol, Atlanta, GA 30322 USA

[12] Emory Univ, Sch Med, Dept Neurol, Atlanta, GA 30322 USA

[13] Emory Univ, Sch Med, Dept Neurol Surg, Atlanta, GA USA

[14] Wills Eye Hosp & Res Inst, Neuroophthalmol Serv, Philadelphia, PA USA

[15] Bellaria Hosp, IRCCS Inst Neurol Sci Bologna, Bologna, Italy

[16] Univ Bologna, Neurol Unit, Dept Biomed & Neuromotor Sci DIBINEM, Bologna, Italy

[17] GenSight Biol, Paris, France

[18] Sorbonne Univ, Inst Vis, Paris, France

[19] Univ Pittsburgh, Sch Med, Dept Ophthalmol, Pittsburgh, PA 15261 USA

来源：

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2019年 / 60卷 / 09期

关键词：

D O I：

暂无

中图分类号：

R77 [眼科学];

学科分类号：

100212 ;

摘要：

4806

引用

页数：4

共 39 条

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