rAAV2/2-ND4 for the Treatment of Leber Hereditary Optic Neuropathy (LHON): 72-Week Data from the REVERSE Phase III Clinical Trial

被引：0
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作者：
Yu-Wai-Man, Patrick [1 ,2 ]
Moster, Mark [3 ,4 ,5 ]
Sadun, Alfredo A. [6 ,7 ]
Klopstock, Thomas [8 ]
Vignal-Clermont, Catherine [9 ,10 ]
Newman, Nancy J. [11 ,12 ,13 ]
Sergott, Robert C. [14 ]
Carelli, Valerio [15 ,16 ]
Chevalier, Caroline [17 ]
Blouin, Laure [17 ]
Taiel, Magali [17 ]
Katz, Barrett [17 ]
Sahel, Jose Alain [18 ,19 ]
机构：
[1] Univ Cambridge, Dept Clin Neurosci, Cambridge, England
[2] Moorfields Eye Hosp, London, England
[3] Wills Eye Hosp & Res Inst, Dept Neuroophthalmol, Philadelphia, PA USA
[4] Thomas Jefferson Univ, Dept Neurol, Sidney Kimmel Med Coll, Philadelphia, PA 19107 USA
[5] Thomas Jefferson Univ, Dept Ophthalmol, Sidney Kimmel Med Coll, Philadelphia, PA 19107 USA
[6] Doheny Eye Inst, 1355 San Pablo St, Los Angeles, CA 90033 USA
[7] Univ Calif Los Angeles, Dept Ophthalmol, Los Angeles, CA USA
[8] Ludwig Maximilians Univ Munchen, Friedrich Baur Inst, Dept Neurol, Munich, Germany
[9] Ctr Hosp Natl Ophtalmol Quinze Vingts, Paris, France
[10] Fdn Ophtalmol Rothschild, Paris, France
[11] Emory Univ, Sch Med, Dept Ophthalmol, Atlanta, GA 30322 USA
[12] Emory Univ, Sch Med, Dept Neurol, Atlanta, GA 30322 USA
[13] Emory Univ, Sch Med, Dept Neurol Surg, Atlanta, GA USA
[14] Wills Eye Hosp & Res Inst, Neuroophthalmol Serv, Philadelphia, PA USA
[15] Bellaria Hosp, IRCCS Inst Neurol Sci Bologna, Bologna, Italy
[16] Univ Bologna, Neurol Unit, Dept Biomed & Neuromotor Sci DIBINEM, Bologna, Italy
[17] GenSight Biol, Paris, France
[18] Sorbonne Univ, Inst Vis, Paris, France
[19] Univ Pittsburgh, Sch Med, Dept Ophthalmol, Pittsburgh, PA 15261 USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2019年 / 60卷 / 09期
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D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
4806
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页数：4
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